Diaphragm pacing and independent breathing in individuals with severe Pompe disease by Cristina Liberati, Barry J. Byrne, David D. Fuller, David D. Fuller, Chasen Croft, Teresa Pitts, Teresa Pitts, Jessica Ehrbar, Carmen Leon-Astudillo, Barbara K. Smith, Barbara K. Smith, Barbara K. Smith

Connect to this object online.

Switching treatment to cipaglucosidase alfa plus miglustat positively affects patient-reported outcome measures in patients with late-onset Pompe disease by Priya S. Kishnani, Barry J. Byrne, Kristl G. Claeys, Jordi Díaz-Manera, Mazen M. Dimachkie, Hani Kushlaf, Tahseen Mozaffar, Mark Roberts, Benedikt Schoser, Noemi Hummel, Agnieszka Kopiec, Fred Holdbrook, Simon Shohet, Antonio Toscano, on behalf of the PROPEL Study Group

Connect to this object online.