Drug Repurposing for Rare Diseases: A Role for Academia by Sibren van den Berg, Sibren van den Berg, Saco de Visser, Hubert G.M. Leufkens, Carla E.M. Hollak, Carla E.M. Hollak

Connect to this object online.

Product Validation and Stability Testing of Pharmacy Compounded Cholic Acid Capsules for Dutch Patients with Rare Bile Acid Synthesis Defects by Yasmin Polak, Bart A. W. Jacobs, Natalja Bouwhuis, Carla E. M. Hollak, Maurice A. G. M. Kroon, Elles Marleen Kemper

Connect to this object online.

Access to medicines for rare diseases: A European regulatory roadmap for academia by Noa Rosenberg, Noa Rosenberg, Sibren van den Berg, Sibren van den Berg, Nina N. Stolwijk, Nina N. Stolwijk, Bart A. W. Jacobs, Bart A. W. Jacobs, Bart A. W. Jacobs, Hendrika C. Post, Hendrika C. Post, Anna M. G. Pasmooij, Anna M. G. Pasmooij, Saco J. de Visser, Saco J. de Visser, Carla E. M. Hollak, Carla E. M. Hollak

Connect to this object online.

Development of a Biosimilar of Agalsidase Beta for the Treatment of Fabry Disease: Preclinical Evaluation by André B. P. van Kuilenburg, Carla E. M. Hollak, Ana Travella, Melisa Jacobs, Lucas D. Gentilini, René Leen, Karen M. M. Ghauharali-van der Vlugt, Femke S. Beers Stet, Susan M. I. Goorden, Sanne van der Veen, Marcelo Criscuolo, Mariana Papouchado

Connect to this object online.