Ngā hua rapu - Christopher Grunseich
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Targeting the 5' untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy mā Audrey M. Winkelsas, Christopher Grunseich, George G. Harmison, Katarzyna Chwalenia, Carlo Rinaldi, Suzan M. Hammond, Kory Johnson, Melissa Bowerman, Sukrat Arya, Kevin Talbot, Matthew J. Wood, Kenneth H. Fischbeck
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