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Antisense Oligonucleotide- and CRISPR-Cas9-Mediated Rescue of mRNA Splicing for a Deep Intronic CLRN1 Mutation by Anna-Lena Panagiotopoulos, Nina Karguth, Marina Pavlou, Sybille Böhm, Gilles Gasparoni, Jörn Walter, Alexander Graf, Helmut Blum, Martin Biel, Lisa Maria Riedmayr, Elvir Becirovic
Published 2020Connect to this object online.
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