Search Results - Joan Bertolin
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1
Progressive neurologic and somatic disease in a novel mouse model of human mucopolysaccharidosis type IIIC by Sara Marcó, Anna Pujol, Carles Roca, Sandra Motas, Albert Ribera, Miguel Garcia, Maria Molas, Pilar Villacampa, Cristian S. Melia, Víctor Sánchez, Xavier Sánchez, Joan Bertolin, Jesús Ruberte, Virginia Haurigot, Fatima Bosch
Published 2016Call Number: Loading…Connect to this object online.
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2
Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy by Sergio Muñoz, Joan Bertolin, Veronica Jimenez, Maria Luisa Jaén, Miquel Garcia, Anna Pujol, Laia Vilà, Victor Sacristan, Elena Barbon, Giuseppe Ronzitti, Jihad El Andari, Warut Tulalamba, Quang Hong Pham, Jesus Ruberte, Thierry VandenDriessche, Marinee K. Chuah, Dirk Grimm, Federico Mingozzi, Fatima Bosch
Published 2024Call Number: Loading…Connect to this object online.
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