Orphan Drugs, Compounded Medication and Pharmaceutical Commons by Kim Hendrickx, Marc Dooms

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Orphan Medicine Incentives: How to Address the Unmet Needs of Rare Disease Patients by Optimizing the European Orphan Medicinal Product Landscape Guiding Principles and Policy Prop... by Annemieke Aartsma-Rus, Marc Dooms, Yann Le Cam

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A Comparative Analysis of Pricing and Reimbursement of Cystic Fibrosis Transmembrane Conductance Regulator Modulators in Europe by Khadidja Abdallah, Kris De Boeck, Marc Dooms, Steven Simoens

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Editorial: Prevention, diagnosis and treatment of rare disorders by Timothy M. Cox, Anna Tylki-Szymańska, Ségolène Aymé, Marc Dooms

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Clinical Research in Neonates: Redesigning the Informed Consent Process in the Digital Era by Evelien De Sutter, Birte Coopmans, Femke Vanendert, Marc Dooms, Karel Allegaert, Karel Allegaert, Karel Allegaert, Pascal Borry, Isabelle Huys

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Clinical and non-clinical aspects of reimbursement policy for orphan drugs in selected European countries by Szczepan Jakubowski, Przemysław Holko, Rafał Nowak, Marisa Warmuth, Marc Dooms, Outi Salminen, Lucas Cortial, Gisbert W. Selke, Christina Georgi, Einar Magnússon, Salvatore Crisafulli, Fons Strijbosch, Tanja Mueller, Eleanor Grieve, Immaculada Danés, Paweł Kawalec

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Reimbursement Status and Recommendations Related to Orphan Drugs in European Countries by Ewa Stawowczyk, Krzysztof Piotr Malinowski, Paweł Kawalec, Rafał Bobiński, Jacek Siwiec, Dimitra Panteli, Dimitra Panteli, Dimitra Panteli, Helene Eckhardt, Helene Eckhardt, Helene Eckhardt, Steven Simoens, Antònia Agusti, Antònia Agusti, Marc Dooms, Andrzej Pilc, Andrzej Pilc

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