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Melanie Kraft
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Allele-specific targeting of mutant ataxin-3 by antisense oligonucleotides in SCA3-iPSC-derived neurons
by
Stefan Hauser
,
Jacob Helm
,
Melanie Kraft
,
Milena Korneck
,
Jeannette Hübener-Schmid
,
Ludger Schöls
Published 2022
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