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Effective AAV-mediated gene replacement therapy in retinal organoids modeling AIPL1-associated LCA4 by Hali Sai, Bethany Ollington, Farah O. Rezek, Niuzheng Chai, Amelia Lane, Anastasios Georgiadis, James Bainbridge, Michel Michaelides, Almudena Sacristan-Reviriego, Pedro R.L. Perdigão, Amy Leung, Jacqueline van der Spuy
Published 2024Connect to this object online.
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