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Block or degrade? Balancing on- and off-target effects of antisense strategies against transcripts with expanded triplet repeats in DM1 by Najoua El Boujnouni, M. Leontien van der Bent, Marieke Willemse, Peter A.C. 't Hoen, Roland Brock, Derick G. Wansink
Published 2023Connect to this object online.
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