Search Results - Priya S. Kishnani
- Showing 1 - 4 results of 4
-
1
Characterization of a canine model of glycogen storage disease type IIIa by Haiqing Yi, Beth L. Thurberg, Sarah Curtis, Stephanie Austin, John Fyfe, Dwight D. Koeberl, Priya S. Kishnani, Baodong Sun
Published 2012Call Number: Loading…Connect to this object online.
Located: Loading…
Book -
2
Use of the patient-reported outcomes measurement information system (PROMIS®) to assess late-onset Pompe disease severity by Melodi Harfouche, Priya S. Kishnani, Eva Krusinska, Jamie Gault, Sheela Sitaraman, Amanda Sowinski, Irina Katz, Stephanie Austin, Margi Goldstein, Andrew E. Mulberg
Published 2020Call Number: Loading…Connect to this object online.
Located: Loading…
Book -
3
Validation of the Patient-Reported Outcomes Measurement Information System (PROMIS®) physical function questionnaire in late-onset Pompe disease using PROPEL phase 3 data by Priya S. Kishnani, Simon Shohet, Syed Raza, Noemi Hummel, Jeffrey P. Castelli, Sheela Sitaraman Das, Heng Jiang, Agnieszka Kopiec, Ian Keyzor, Andreas Hahn
Published 2024Call Number: Loading…Connect to this object online.
Located: Loading…
Book -
4
Switching treatment to cipaglucosidase alfa plus miglustat positively affects patient-reported outcome measures in patients with late-onset Pompe disease by Priya S. Kishnani, Barry J. Byrne, Kristl G. Claeys, Jordi Díaz-Manera, Mazen M. Dimachkie, Hani Kushlaf, Tahseen Mozaffar, Mark Roberts, Benedikt Schoser, Noemi Hummel, Agnieszka Kopiec, Fred Holdbrook, Simon Shohet, Antonio Toscano, on behalf of the PROPEL Study Group
Published 2024Call Number: Loading…Connect to this object online.
Located: Loading…
Book