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Shih-Hsin Kan
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Shih-Hsin Kan
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Shih-Hsin Kan
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1
Base editing rescues acid α-glucosidase function in infantile-onset Pompe disease patient-derived cells
by
Chloe L. Christensen
,
Shih-Hsin Kan
,
Perla Andrade-Heckman
,
Allisandra K. Rha
,
Jerry F. Harb
,
Raymond Y. Wang
Published 2024
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2
Base editing corrects the common Salla disease SLC17A5 c.115C>T variant
by
Jerry F. Harb
,
Chloe L. Christensen
,
Shih-Hsin Kan
,
Allisandra K. Rha
,
Perla Andrade-Heckman
,
Laura Pollard
,
Richard Steet
,
Jeffrey Y. Huang
,
Raymond Y. Wang
Published 2023
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