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GAA Deficiency in Pompe Disease Is Alleviated by Exon Inclusion in iPSC-Derived Skeletal Muscle Cells by Erik van der Wal, Atze J. Bergsma, Tom J.M. van Gestel, Stijn L.M. in 't Groen, Holm Zaehres, Marcos J. Araúzo-Bravo, Hans R. Schöler, Ans T. van der Ploeg, W.W.M. Pim Pijnappel
Published 2017Connect to this object online.
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