Cover Image

CRISPR-Cas9-directed gene therapy for spinocerebellar ataxia type 1

Saved in:

Bibliographic Details
Main Authors:	Mihai Miclăuș (Author), Gabriel Balmus (Author)
Format:	Book
Published:	Elsevier, 2024-12-01T00:00:00Z.
Subjects:	article
Online Access:	Connect to this object online.
Tags:	Add Tag No Tags, Be the first to tag this record!

Similar Items

Cas9 editing of ATXN1 in a spinocerebellar ataxia type 1 mice and human iPSC-derived neurons
by: Kelly J. Fagan, et al.
Published: (2024)

Spinocerebellar Ataxia
Published: (2012)

Spinocerebellar Ataxia
by: J Gordon Millichap
Published: (1988)

Epilepsy and Spinocerebellar Ataxia
by: J Gordon Millichap
Published: (2007)

Spinocerebellar Ataxia Concepts, Particularities and Generalities
Published: (2022)

Spinocerebellar Ataxia 21 with Retardation
by: J Gordon Millichap, et al.
Published: (2014)

Clinical-cognitive Characterization of Spinocerebellar Ataxia Type 2
by: Alberto Caballero Laguna, et al.
Published: (2021)

Clinical-cognitive Characterization of Spinocerebellar Ataxia Type 2
by: Alberto Caballero Laguna, et al.
Published: (2021)

CRISPR-Cas9 for in vivo Gene Therapy: Promise and Hurdles
by: Wei-Jing Dai, et al.
Published: (2016)

CRISPR-Cas9-mediated homology-directed repair for precise gene editing
by: Hongyu Liao, et al.
Published: (2024)

Characteristics of Individuals at Risk for Spinocerebellar Ataxia
by: J Gordon Millichap
Published: (2013)

Gene editing and therapy - A new tool: CRISPR/Cas9
by: Ashok M. Patil
Published: (2019)

New Perspectives of Gene Therapy on Polyglutamine Spinocerebellar Ataxias: From Molecular Targets to Novel Nanovectors
by: Fabiola V. Borbolla-Jiménez, et al.
Published: (2021)

Respiratory dysfunction in a mouse model of spinocerebellar ataxia type 7
by: Anna F. Fusco, et al.
Published: (2021)

A Novel Anti-Cancer Therapy: CRISPR/Cas9 Gene Editing
by: Xin-Zhu Chen, et al.
Published: (2022)

Overcoming the Undesirable CRISPR-Cas9 Expression in Gene Correction
by: Emily Xia, et al.
Published: (2018)

A Difficult Case to Diagnose: Machado-Joseph Disease/Spinocerebellar Ataxia Type III
by: Muhammad Sohail Ajmal Ghoauri, et al.
Published: (2023)

Antisense Oligonucleotide-Mediated Removal of the Polyglutamine Repeat in Spinocerebellar Ataxia Type 3 Mice
by: Lodewijk J.A. Toonen, et al.
Published: (2017)

Cerebellar neuronal dysfunction accompanies early motor symptoms in spinocerebellar ataxia type 3
by: Kristin Mayoral-Palarz, et al.
Published: (2022)

Application of CRISPR-Cas9 gene editing for congenital heart disease
by: Heeyoung Seok, et al.
Published: (2021)

CRISPR-Cas9 mediated phage therapy as an alternative to antibiotics
by: Fikre Birhanu Balcha, et al.
Published: (2023)

CRISPR-Cas9 gene editing strengthens cuproptosis/chemodynamic/ferroptosis synergistic cancer therapy
by: Xiaoyu Wu, et al.
Published: (2024)

CRISPR-Cas9-directed gene tagging using a single integrase-defective lentiviral vector carrying a transposase-based Cas9 off switch
by: Emil Aagaard Thomsen, et al.
Published: (2022)

Application of CRISPR/Cas9 in plant biology
by: Xuan Liu, et al.
Published: (2017)

In Vitro Efficacy and Molecular Mechanism of Curcumin Analog in Pathological Regulation of Spinocerebellar Ataxia Type 3
by: Yu-Ling Wu, et al.
Published: (2022)

Optimization of sand fly embryo microinjection for gene editing by CRISPR/Cas9.
by: Ines Martin-Martin, et al.
Published: (2018)

CRISPR-Cas9 delivery strategies with engineered extracellular vesicles
by: Yaoyao Lu, et al.
Published: (2023)

CRISPR/Cas9-Mediated Customizing Strategies for Adoptive T-Cell Therapy
by: Hyeseon Park, et al.
Published: (2024)

Research progress of gene editing technology CRISPR/Cas9 system in animal gene editing
by: Feng Fan, et al.
Published: (2018)

Elimination of HIV-1 genomes from human T-lymphoid cells by CRISPR/Cas9 gene editing
by: K. Khalili, et al.
Published: (2015)

Inhibition of adenovirus replication by CRISPR-Cas9-mediated targeting of the viral E1A gene
by: Zrinka Didara, et al.
Published: (2023)

The Chromatin Structure of CRISPR-Cas9 Target DNA Controls the Balance between Mutagenic and Homology-Directed Gene-Editing Events
by: Josephine M. Janssen, et al.
Published: (2019)

CRISPR-Cas9-Based Technology and Its Relevance to Gene Editing in Parkinson's Disease
by: Mujeeb ur Rahman, et al.
Published: (2022)

CRISPR/Cas9: Transcending the Reality of Genome Editing
by: Sergiu Chira, et al.
Published: (2017)

Targeting Hepatitis B Virus With CRISPR/Cas9
by: Christoph Seeger, et al.
Published: (2014)

The CRISPR/Cas9 System Delivered by Extracellular Vesicles
by: Xinglong Zhu, et al.
Published: (2023)

Generation of desminopathy in rats using CRISPR‐Cas9
by: Henning T. Langer, et al.
Published: (2020)

Mangifera indica L. extract (Vimang) improves the aversive memory in spinocerebellar ataxia type 2 transgenic mice.
by: Natasha Maurmann, et al.
Published: (2014)

Blood levels of neurofilament light are associated with disease progression in a mouse model of spinocerebellar ataxia type 3
by: David Mengel, et al.
Published: (2023)

Utilizing the binding capacity of CRISPR/Cas9 to target the HIV-1 quasispecies
by: M. Nonnemacher, et al.
Published: (2015)