Long-Term Morpholino Oligomers in Hexose Elicits Long-Lasting Therapeutic Improvements in mdx Mice
Approval of antisense oligonucleotide eteplirsen highlights the promise of exon-skipping therapeutics for Duchenne muscular dystrophy patients. However, the limited efficacy of eteplirsen underscores the importance to improve systemic delivery and efficacy. Recently, we demonstrated that a glucose a...
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| Main Authors: | , , , , |
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| Format: | Book |
| Published: |
Elsevier,
2018-09-01T00:00:00Z.
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| Subjects: | |
| Online Access: | Connect to this object online. |
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