Therapeutic Strategies For Tay-Sachs Disease
Tay-Sachs disease (TSD) is an autosomal recessive disease that features progressive neurodegenerative presentations. It affects one in 100,000 live births. Currently, there is no approved therapy or cure. This review summarizes multiple drug development strategies for TSD, including enzyme replaceme...
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Main Authors: | Jaqueline A. Picache (Author), Wei Zheng (Author), Catherine Z. Chen (Author) |
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Format: | Book |
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Frontiers Media S.A.,
2022-07-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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