Gene Therapy for Mitochondrial Diseases: Current Status and Future Perspective
Mitochondrial diseases (MDs) are a group of severe genetic disorders caused by mutations in the nuclear or mitochondrial genome encoding proteins involved in the oxidative phosphorylation (OXPHOS) system. MDs have a wide range of symptoms, ranging from organ-specific to multisystemic dysfunctions, w...
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Main Authors: | Alessia Di Donfrancesco (Author), Giulia Massaro (Author), Ivano Di Meo (Author), Valeria Tiranti (Author), Emanuela Bottani (Author), Dario Brunetti (Author) |
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Format: | Book |
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MDPI AG,
2022-06-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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