Efficacy of Postnatal In Vivo Nonsense Suppression Therapy in a Pax6 Mouse Model of Aniridia
Nonsense mutations leading to premature stop codons are common occurring in approximately 12% of all human genetic diseases. Thus, pharmacological nonsense mutation suppression strategies would be beneficial to a large number of patients if the drugs could be targeted to the affected tissues at the...
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| Main Authors: | , , , , , |
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| Format: | Book |
| Published: |
Elsevier,
2017-06-01T00:00:00Z.
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| Online Access: | Connect to this object online. |
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