Development of idursulfase therapy for mucopolysaccharidosis type II (Hunter syndrome): the past, the present and the future
David AH Whiteman,* Alan Kimura* Research & Development, Shire Human Genetic Therapies, Inc., Lexington, MA, USA *These authors contributed equally to this work Abstract: Mucopolysaccharidosis type II (MPS II; Hunter syndrome; OMIM 309900) is a rare, multisystemic, progressive lysosomal...
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Main Authors: | Whiteman DAH (Author), Kimura A (Author) |
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Format: | Book |
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Dove Medical Press,
2017-08-01T00:00:00Z.
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