Riboswitches for Controlled Expression of Therapeutic Transgenes Delivered by Adeno-Associated Viral Vectors
Vectors developed from adeno-associated virus (AAV) are powerful tools for in vivo transgene delivery in both humans and animal models, and several AAV-delivered gene therapies are currently approved for clinical use. However, AAV-mediated gene therapy still faces several challenges, including limit...
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Main Authors: | Zachary J. Tickner (Author), Michael Farzan (Author) |
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Format: | Book |
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MDPI AG,
2021-06-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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Correction: Tickner, Z.J.; Farzan, M. Riboswitches for Controlled Expression of Therapeutic Transgenes Delivered by Adeno-Associated Viral Vectors. <i>Pharmaceuticals</i> 2021, <i>14</i>, 554
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