Disease progression modeling of the North Star Ambulatory Assessment for Duchenne Muscular Dystrophy
Abstract Duchenne muscular dystrophy (DMD) is a rare genetic disorder caused by decreased or absent dystrophin gene leading to progressive muscle degeneration and weakness in young boys. Disease progression models for the North Star Ambulatory Assessment (NSAA), a functional measurement widely used...
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Wiley,
2023-03-01T00:00:00Z.
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