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In Vitro Studies to Evaluate the Intestinal Permeation of an Ursodeoxycholic Acid-Conjugated Oligonucleotide for Duchenne Muscular Dystrophy Treatment

Delivery represents a major hurdle to the clinical advancement of oligonucleotide therapeutics for the treatment of disorders such as Duchenne muscular dystrophy (DMD). In this preliminary study, we explored the ability of 2'-<i>O</i>-methyl-phosphorothioate antisense oligonucleotid...

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Wedi'i Gadw mewn:

Manylion Llyfryddiaeth
Prif Awduron:	Marika Faiella (Awdur), Giada Botti (Awdur), Alessandro Dalpiaz (Awdur), Lorenzo Gnudi (Awdur), Aurélie Goyenvalle (Awdur), Barbara Pavan (Awdur), Daniela Perrone (Awdur), Matteo Bovolenta (Awdur), Elena Marchesi (Awdur)
Fformat:	Llyfr
Cyhoeddwyd:	MDPI AG, 2024-08-01T00:00:00Z.
Pynciau:	article
Mynediad Ar-lein:	Connect to this object online.
Tagiau:	Ychwanegu Tag Dim Tagiau, Byddwch y cyntaf i dagio'r cofnod hwn!

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