Cost-effectiveness of voretigene neparvovec in the treatment of patients with inherited retinal disease with RPE65 mutation in Switzerland
Abstract Objective We aimed to evaluate the cost-effectiveness of voretigene neparvovec (VN) compared with standard of care (SoC) for patients with inherited retinal disease (IRD) caused by a biallelic RPE65-mutation. VN is a live, non-replicating adeno-associated virus serotype 2 (AAV2). SoC is bes...
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Main Authors: | Arjun Bhadhuri (Author), Daniel Dröschel (Author), Mike Guldimann (Author), Claudia Jetschgo (Author), Judit Banhazi (Author), Matthias Schwenkglenks (Author), C. Simone Sutherland (Author) |
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Format: | Book |
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BMC,
2022-06-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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