Search Results - "Exon skipping"

Suggested Topics within your search.
Refine Results
  1. 61
    Cover Image

    Antisense Oligonucleotide-Mediated Removal of the Polyglutamine Repeat in Spinocerebellar Ataxia Type 3 Mice by Lodewijk J.A. Toonen, Frank Rigo, Haico van Attikum, Willeke M.C. van Roon-Mom

    Published 2017
    Connect to this object online.
    Book

    Save to List
    Saved in:
  2. 62
    Cover Image

    Cationic Oligospermine-Oligonucleotide Conjugates Provide Carrier-free Splice Switching in Monolayer Cells and Spheroids by Marc Nothisen, Phanélie Perche-Létuvée, Jean-Paul Behr, Jean-Serge Remy, Mitsuharu Kotera

    Published 2018
    Connect to this object online.
    Book

    Save to List
    Saved in:
  3. 63
    Cover Image

    Single-swap editing for the correction of common Duchenne muscular dystrophy mutations by Andreas C. Chai, Francesco Chemello, Hui Li, Takahiko Nishiyama, Kenian Chen, Yu Zhang, Efraín Sánchez-Ortiz, Adeeb Alomar, Lin Xu, Ning Liu, Rhonda Bassel-Duby, Eric N. Olson

    Published 2023
    Connect to this object online.
    Book

    Save to List
    Saved in:
  4. 64
    Cover Image

    The use of genetically humanized animal models for personalized medicine approaches by Annemieke Aartsma-Rus, Maaike van Putten, Annemieke Aartsma-Rus, James Dowling, Maaike van Putten

    Published 2020
    Connect to this object online.
    Book

    Save to List
    Saved in:
  5. 65
    Cover Image

    Anti-inflammatory drugs for Duchenne muscular dystrophy: focus on skeletal muscle-releasing factors by Miyatake S, Shimizu-Motohashi Y, Takeda S, Aoki Y

    Published 2016
    Connect to this object online.
    Book

    Save to List
    Saved in:
  6. 66
    Cover Image

    Systemic PPMO-mediated dystrophin expression in the Dup2 mouse model of Duchenne muscular dystrophy by Liubov V. Gushchina, Tatyana A. Vetter, Emma C. Frair, Adrienne J. Bradley, Kelly M. Grounds, Jacob W. Lay, Nianyuan Huang, Aisha Suhaiba, Frederick J. Schnell, Gunnar Hanson, Tabatha R. Simmons, Nicolas Wein, Kevin M. Flanigan

    Published 2022
    Connect to this object online.
    Book

    Save to List
    Saved in:
  7. 67
    Cover Image

    Theragnosis for Duchenne Muscular Dystrophy by Leonela Luce, Leonela Luce, Micaela Carcione, Micaela Carcione, Chiara Mazzanti, Chiara Mazzanti, Paula I. Buonfiglio, Viviana Dalamón, Lilia Mesa, Alberto Dubrovsky, José Corderí, Florencia Giliberto, Florencia Giliberto

    Published 2021
    Connect to this object online.
    Book

    Save to List
    Saved in:
  8. 68
    Cover Image

    Saponins as Natural Adjuvant for Antisense Morpholino Oligonucleotides Delivery In Vitro and in mdx Mice by Mingxing Wang, Bo Wu, Sapana N. Shah, Peijuan Lu, Qilong Lu

    Published 2018
    Connect to this object online.
    Book

    Save to List
    Saved in:
  9. 69
    Cover Image

    Endometrial gland-specific progestagenassociated endometrial protein and cilia gene splicing changes in recurrent pregnancy loss by Jennifer E Pearson-Farr, Gabrielle Wheway, Maaike S A Jongen, Patricia Goggin, Rohan M Lewis, Ying Cheong, Jane K Cleal

    Published 2022
    Connect to this object online.
    Book

    Save to List
    Saved in:
  10. 70
    Cover Image

    Uniform sarcolemmal dystrophin expression is required to prevent extracellular microRNA release and improve dystrophic pathology by Tirsa L.E. vanWestering, Yulia Lomonosova, Anna M.L. Coenen‐Stass, Corinne A. Betts, Amarjit Bhomra, Margriet Hulsker, Lucy E. Clark, Graham McClorey, Annemieke Aartsma‐Rus, Maaike vanPutten, Matthew J.A. Wood, Thomas C. Roberts

    Published 2020
    Connect to this object online.
    Book

    Save to List
    Saved in:
  11. 71
    Cover Image

    Lessons Learned from Discontinued Clinical Developments in Duchenne Muscular Dystrophy by Theodora Markati, Liesbeth De Waele, Liesbeth De Waele, Urlike Schara-Schmidt, Laurent Servais, Laurent Servais

    Published 2021
    Connect to this object online.
    Book

    Save to List
    Saved in:
  12. 72
    Cover Image

    Induced-Decay of Glycine Decarboxylase Transcripts as an Anticancer Therapeutic Strategy for Non-Small-Cell Lung Carcinoma by Jing Lin, Jia Hui Jane Lee, Kathirvel Paramasivam, Elina Pathak, Zhenxun Wang, Zacharias Aloysius Dwi Pramono, Bing Lim, Keng Boon Wee, Uttam Surana

    Published 2017
    Connect to this object online.
    Book

    Save to List
    Saved in:
  13. 73
    Cover Image

    Targeting TGF-β Signaling by Antisense Oligonucleotide-mediated Knockdown of TGF-β Type I Receptor by Dwi U Kemaladewi, Svitlana Pasteuning, Joke W van der Meulen, Sandra H van Heiningen, Gert-Jan van Ommen, Peter ten Dijke, Annemieke Aartsma-Rus, Peter AC 't Hoen, Willem M Hoogaars

    Published 2014
    Connect to this object online.
    Book

    Save to List
    Saved in:
  14. 74
    Cover Image

    Long-Term Morpholino Oligomers in Hexose Elicits Long-Lasting Therapeutic Improvements in mdx Mice by Gang Han, Caorui Lin, Hanhan Ning, Xianjun Gao, HaiFang Yin

    Published 2018
    Connect to this object online.
    Book

    Save to List
    Saved in:
  15. 75
    Cover Image

    Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method by Jean-Paul, Dominique L Ouellet, Xavier Barbeau, Joël Rousseau, Pierre Chapdelaine, Patrick Lagüe, Jacques P Tremblay

    Published 2016
    Connect to this object online.
    Book

    Save to List
    Saved in:
  16. 76
    Cover Image

    Fructose Promotes Uptake and Activity of Oligonucleotides With Different Chemistries in a Context-dependent Manner in mdx Mice by Limin Cao, Gang Han, Caorui Lin, Ben Gu, Xianjun Gao, Hong M Moulton, Yiqi Seow, HaiFang Yin

    Published 2016
    Connect to this object online.
    Book

    Save to List
    Saved in:
  17. 77
    Cover Image

    Electroporation Enhanced Effect of Dystrophin Splice Switching PNA Oligomers in Normal and Dystrophic Muscle by Camilla Brolin, Takehiko Shiraishi, Pernille Hojman, Thomas O Krag, Peter E Nielsen, Julie Gehl

    Published 2015
    Connect to this object online.
    Book

    Save to List
    Saved in:
  18. 78
    Cover Image

    Partial restoration of brain dystrophin by tricyclo-DNA antisense oligonucleotides alleviates emotional deficits in mdx52 mice by Amel Saoudi, Sacha Barberat, Olivier le Coz, Ophélie Vacca, Mathilde Doisy Caquant, Thomas Tensorer, Eric Sliwinski, Luis Garcia, Francesco Muntoni, Cyrille Vaillend, Aurélie Goyenvalle

    Published 2023
    Connect to this object online.
    Book

    Save to List
    Saved in:
  19. 79
    Cover Image

    Molecular and Biochemical Therapeutic Strategies for Duchenne Muscular Dystrophy by Lakshmi Krishna, Akila Prashant, Yogish H. Kumar, Shasthara Paneyala, Siddaramappa J. Patil, Shobha Chikkavaddaragudi Ramachandra, Prashant Vishwanath

    Published 2024
    Connect to this object online.
    Book

    Save to List
    Saved in:
  20. 80
    Cover Image

    Intramuscular Evaluation of Chimeric Locked Nucleic Acid/2'<i>O</i>Methyl-Modified Antisense Oligonucleotides for Targeted Exon 23 Skipping in Mdx Mice by Michaella Georgiadou, Melina Christou, Kleitos Sokratous, Jesper Wengel, Kyriaki Michailidou, Kyriacos Kyriacou, Andrie Koutsoulidou, Nikolaos P. Mastroyiannopoulos, Leonidas A. Phylactou

    Published 2021
    Connect to this object online.
    Book

    Save to List
    Saved in:

Search Tools: