Search Results - "eteplirsen"

Eteplirsen in the treatment of Duchenne muscular dystrophy by Lim KRQ, Maruyama R, Yokota T

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Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA by Joel Iff, Yi Zhon, Edward Tuttle, Deepshekhar Gupta, Xander Paul, Erik Henricson

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Understanding Neuromuscular Health and Disease: Advances in Genetics, Omics, and Molecular Function

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Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD by Ugur Akpulat, Haicui Wang, Kerstin Becker, Adriana Contreras, Terence A. Partridge, James S. Novak, Sebahattin Cirak

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Antisense Oligonucleotides: Concepts and Pharmaceutical Applications by Ariana Araya, David Arias, Karla Coto, María Rebeca López, Joselyn Rivera, Juan José Mora

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Long-Term Morpholino Oligomers in Hexose Elicits Long-Lasting Therapeutic Improvements in mdx Mice by Gang Han, Caorui Lin, Hanhan Ning, Xianjun Gao, HaiFang Yin

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Therapeutic targeting of alternative splicing by Jarosław Paluszczak

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Recent Trends in Antisense Therapies for Duchenne Muscular Dystrophy by Harry Wilton-Clark, Toshifumi Yokota

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