Search Results - "gene therapies"

Managing the challenges of paying for gene therapy: strategies for market action and policy reform in the United States by Sharon Phares, Mark Trusheim, Sarah K Emond, Steven D Pearson

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Hepatic gene therapy rescues high-fat diet responses in circadian Clock mutant mice by Judit Meyer-Kovac, Isa Kolbe, Lea Ehrhardt, Alexei Leliavski, Jana Husse, Gabriela Salinas, Thomas Lingner, Anthony H. Tsang, Johanna L. Barclay, Henrik Oster

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Economic outcomes of centralized procurements of gene therapy for patients with orphan diseases: inherited retinal dystrophy by N. А. Avxentyev, Yu. V. Makarova, V. V. Kadyshev

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How are health technology assessment bodies responding to the assessment challenges posed by cell and gene therapy? by Michael Drummond, Oriana Ciani, Giulia Fornaro, Claudio Jommi, Eva Susanne Dietrich, Jaime Espin, Jean Mossman, Gerard de Pouvourville

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Development of Lentiviral Vectors for HIV-1 Gene Therapy with Vif-Resistant APOBEC3G by Krista A. Delviks-Frankenberry, Daniel Ackerman, Nina D. Timberlake, Maria Hamscher, Olga A. Nikolaitchik, Wei-Shau Hu, Bruce E. Torbett, Vinay K. Pathak

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The Multifaceted Role of Extracellular Vesicles in Glioblastoma: microRNA Nanocarriers for Disease Progression and Gene Therapy by Natalia Simionescu, Radu Zonda, Anca Roxana Petrovici, Adriana Georgescu

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A Nanoparticle Delivery of Plasmid Encoding Hepatocyte Growth Factor for Gene Therapy of Silicosis in Mice by Haiying Duan, Peng Gao, Xiaochen Cheng, Yuxin Lu, Chunsheng Hu, Xuefeng Zhu, Xiaoying Wang, Dujuan Li, Fengjun Xiao, Li Du, Yunmei Liu, Qinglin Zhang

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A New Gene Therapy Approach for Cardiovascular Disease by Non-coding RNAs Acting in the Nucleus by Tiia Husso, Seppo Ylä-Herttuala, Mikko P Turunen

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Consensus Statement from the First International Conference for In Utero Stem Cell Transplantation and Gene Therapy by Tippi C. Mackenzie

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Ultrasound-mediated gene delivery of factor VIII plasmids for hemophilia A gene therapy in mice by Shuxian Song, Meghan J. Lyle, Misty L. Noble-Vranish, Dominic M. Min-Tran, James Harrang, Weidong Xiao, Evan C. Unger, Carol H. Miao

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Validation of Gene Therapy for Mutant Mitochondria by Delivering Mitochondrial RNA Using a MITO-Porter by Eriko Kawamura, Minako Maruyama, Jiro Abe, Akira Sudo, Atsuhito Takeda, Shingo Takada, Takashi Yokota, Shintaro Kinugawa, Hideyoshi Harashima, Yuma Yamada

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α-Galactosidase A Augmentation by Non-Viral Gene Therapy: Evaluation in Fabry Disease Mice by Julen Rodríguez-Castejón, Ana Alarcia-Lacalle, Itziar Gómez-Aguado, Mónica Vicente-Pascual, María Ángeles Solinís Aspiazu, Ana del Pozo-Rodríguez, Alicia Rodríguez-Gascón

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The oncogenic roles of GPR176 in ovarian cancer: a molecular target for aggressiveness and gene therapy by Ning Yang, Wen-jing Yun, Zheng-guo Cui, Hua-chuan Zheng

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Outcome Measures Used in Ocular Gene Therapy Trials: A Scoping Review of Current Practice by Jasleen K. Jolly, Jasleen K. Jolly, Jasleen K. Jolly, Holly Bridge, Robert E. MacLaren, Robert E. MacLaren

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BMP4 gene therapy enhances insulin sensitivity but not adipose tissue browning in obese mice by Jenny M. Hoffmann, John R. Grünberg, Ann Hammarstedt, Tobias Kroon, Thomas U. Greiner, Stefanie Maurer, Ivet Elias, Vilborg Palsdottir, Fatima Bosch, Jeremie Boucher, Shahram Hedjazifar, Ulf Smith

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Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy by Shin'ichi Takeda, Takashi Okada

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Chapter From the Molecular Biology to the Gene Therapy of a DNA Repair Syndrome: Fanconi Anemia by Bueren, Juan A.

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Improving access to gene therapies: a holistic view of current challenges and future policy solutions in the United States by Tyler D Wagner, Lisabeth Buelt, Kimberly Westrich, Jonathan D Campbell

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Oral Gene Therapy of HFD-Obesity via Nonpathogenic Yeast Microcapsules Mediated shRNA Delivery by Li Zhang, Wan Zhang, Hang Peng, Yankun Li, Tongtong Leng, Chenxi Xie, Long Zhang

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Intra-articular lentivirus-mediated gene therapy targeting CRACM1 for the treatment of collagen-induced arthritis by Shuang Liu, Takeshi Kiyoi, Erika Takemasa, Kazutaka Maeyama

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