Search Results - "gene therapies"

Assessing the value of delandistrogene moxeparvovec (SRP-9001) gene therapy in patients with Duchenne muscular dystrophy in the United States by Alexa C. Klimchak, Lauren E. Sedita, Louise R. Rodino-Klapac, Jerry R. Mendell, Craig M. McDonald, Katherine L. Gooch, Daniel C. Malone

Connect to this object online.

Annuity payments can increase patient access to innovative cell and gene therapies under England's net budget impact test by Jesper Jørgensen, Panos Kefalas

Connect to this object online.

Design and Evaluation of Gemini Surfactant-Based Lipoplexes Modified with Cell-Binding Peptide for Targeted Gene Therapy in Melanoma Model by Waleed Mohammed-Saeid, Rania Soudy, Richa Tikoo, Kamaljit Kaur, Ronald E Verrall, Ildiko Badea

Connect to this object online.

Clustered regularly interspaced short palindromic repeats-Cas9 gene therapy: The top 50 most-cited papers by Jude Howaidi, Ali Howaidi, Faisal Howaidi

Connect to this object online.

Optimization of a lentivirus-mediated gene therapy targeting HIV-1 RNA to eliminate HIV-1-infected cells by Amanda B. Buckingham, Sophia Ho, Finlay Knops-Mckim, Carin K. Ingemarsdotter, Andrew M.L. Lever

Connect to this object online.

Cellular Reprogramming, Genome Editing, and Alternative CRISPR Cas9 Technologies for Precise Gene Therapy of Duchenne Muscular Dystrophy by Peter Gee, Huaigeng Xu, Akitsu Hotta

Connect to this object online.

Klotho and Mesenchymal Stem Cells: A Review on Cell and Gene Therapy for Chronic Kidney Disease and Acute Kidney Disease by Marcella Liciani Franco, Stephany Beyerstedt, Érika Bevilaqua Rangel

Connect to this object online.

Mesenchymal Stem Cell-Based NK4 Gene Therapy in Nude Mice Bearing Gastric Cancer Xenografts [Corrigendum] by Zhu Y, Cheng M, Yang Z, Zeng C, Chen J, Xie Y, Luo S, Zhang K, Zhou S, Lu N

Connect to this object online.

Adeno-associated virus-based gene therapy delivering combinations of two growth-associated genes to MPS IVA mice by Estera Rintz, Betul Celik, Nidhi Fnu, Angélica María Herreño-Pachón, Shaukat Khan, Eliana Benincore-Flórez, Shunji Tomatsu

Connect to this object online.

Targeted suicide gene therapy for liver cancer based on ribozyme-mediated RNA replacement through post-transcriptional regulation by Seung Ryul Han, Chang Ho Lee, Ji Young Im, Ju Hyun Kim, Ji Hyun Kim, Sung Jin Kim, Young Woo Cho, Eunkyung Kim, Youngah Kim, Ji-Ho Ryu, Mi Ha Ju, Jin Sook Jeong, Seong-Wook Lee

Connect to this object online.

Exploiting the Intron-splicing Mechanism of Insect Cells to Produce Viral Vectors Harboring Toxic Genes for Suicide Gene Therapy by Haifeng Chen

Connect to this object online.

The Application of Induced Pluripotent Stem Cells in Pathogenesis Study and Gene Therapy for Vascular Disorders: Current Progress and Future Challenges by Guang-Yin Peng, Yang Lin, Jing-Jing Li, Ying Wang, Hao-Yue Huang, Zhen-Ya Shen

Connect to this object online.

Targeted Multifunctional Lipid ECO Plasmid DNA Nanoparticles as Efficient Non-viral Gene Therapy for Leber's Congenital Amaurosis by Da Sun, Bhubanananda Sahu, Songqi Gao, Rebecca M. Schur, Amita M. Vaidya, Akiko Maeda, Krzysztof Palczewski, Zheng-Rong Lu

Connect to this object online.

Improved intravenous lentiviral gene therapy based on endothelial-specific promoter-driven factor VIII expression for hemophilia A by Jie Gong, Rui Yang, Min Zhou, Lung-Ji Chang

Connect to this object online.

The Future of Gene Therapy for Transfusion-Dependent Beta-Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells by Parin Rattananon, Usanarat Anurathapan, Kanit Bhukhai, Suradej Hongeng

Connect to this object online.

Novel Pyropheophorbide Phosphatydic Acids Photosensitizer Combined EGFR siRNA Gene Therapy for Head and Neck Cancer Treatment by Chia-Hsien Yeh, Juan Chen, Gang Zheng, Leaf Huang, Yih-Chih Hsu

Connect to this object online.

E-Selectin/AAV Gene Therapy Promotes Myogenesis and Skeletal Muscle Recovery in a Mouse Hindlimb Ischemia Model by Antoine J. Ribieras, Yulexi Y. Ortiz, Yan Li, Nga T. Le, Carlos T. Huerta, Francesca A. Voza, Hongwei Shao, Roberto I. Vazquez-Padron, Zhao-Jun Liu, Omaida C. Velazquez

Connect to this object online.

Fetal Brain-directed AAV Gene Therapy Results in Rapid, Robust, and Persistent Transduction of Mouse Choroid Plexus Epithelia by Marie Reine Haddad, Anthony Donsante, Patricia Zerfas, Stephen G Kaler

Connect to this object online.

Hair cell-specific Myo15 promoter-mediated gene therapy rescues hearing in DFNB9 mouse model by Hui Wang, MengZhao Xun, Honghai Tang, Jingjing Zhao, Shaowei Hu, Longlong Zhang, Jun Lv, Daqi Wang, Yuxin Chen, Jianping Liu, Geng-lin Li, Wuqing Wang, Yilai Shu, Huawei Li

Connect to this object online.

Brain Tumors An Update

Subjects: “…chemotherapy, surgery, gene therapy, targeted therapy, radiotherapy, glioblastoma…”
DOAB: download the publication
DOAB: description of the publication