Search Results - "gene therapies"

Challenges and Opportunities for Effective Cancer Immunotherapies

Subjects: “…gene therapy…”
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Non-Viral Gene Delivery Systems for Treatment of Myocardial Infarction: Targeting Strategies and Cardiac Cell Modulation by Jieting Wang, Luying Yu, Ao Zhou, Jie Liu, Kai Wang, Ying Luo, Fang Wang

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Modality diversification and best-in-class small-molecule drugs: Recent trend of orphan drug development by Ryo Okuyama

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LinQURE: A novel AAV gene silencing platform that supports multi-transcript targeting for complex disorders by Irena Bočkaj, Anna Moreno Garcia, Pablo de Miguel Herraiz, Sonay Keskin, Vanessa Zancanella, Şeyda Acar Broekmans, Astrid Vallès, Ying Poi Liu, Melvin Evers, Morgane Wartel

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Molecular and Biochemical Therapeutic Strategies for Duchenne Muscular Dystrophy by Lakshmi Krishna, Akila Prashant, Yogish H. Kumar, Shasthara Paneyala, Siddaramappa J. Patil, Shobha Chikkavaddaragudi Ramachandra, Prashant Vishwanath

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Acellular scaffolds, cellular therapy and next generation approaches for knee cartilage repair by Pedro Debieux, Enzo Salviato Mameri, Giovanna Medina, Keng Lin Wong, Camila Cohen Keleka

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Preclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic LZTR1 variants by Carolin Knauer, Henrike Haltern, Eric Schoger, Sebastian Kügler, Lennart Roos, Laura C. Zelarayán, Gerd Hasenfuss, Wolfram-Hubertus Zimmermann, Bernd Wollnik, Lukas Cyganek

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Implementation of experimental cellular (cellular-genetic) therapies on the example of eye diseases by Patrycja Kapczuk, Karolina Rogulska, Anna Stangret, Agata Mularczyk, Angelika Szczęśniak, Katarzyna Topczewska, Konrad Grzeszczak

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Microbubble drug conjugate and focused ultrasound blood brain barrier delivery of AAV-2 SIRT-3 by Dennison Trinh, Joanne Nash, David Goertz, Kullervo Hynynen, Sharshi Bulner, Umar Iqbal, James Keenan

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Upgrading the SACT dataset and EBMT registry to enable outcomes-based reimbursement in oncology in England: a gap analysis and top-level cost estimate by Jesper Jørgensen, Panos Kefalas

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PH-Responsive, Cell-Penetrating, Core/Shell Magnetite/Silver Nanoparticles for the Delivery of Plasmids: Preparation, Characterization, and Preliminary In Vitro Evaluation by Carlos M. Ramírez-Acosta, Javier Cifuentes, Maria Claudia Castellanos, Rodolfo José Moreno, Carolina Muñoz-Camargo, Juan C. Cruz, Luis H. Reyes

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Canine Genetics, Health and Medicine

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Prenatal Beginnings for Better Health by Maged Costantine

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From non-invasive to invasive fetal therapy: A comprehensive review and current update by Tzu-Yi Lin, Tuangsit Wataganara, Steven W. Shaw

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Kymriah® (tisagenlecleucel) - An overview of the clinical development journey of the first approved CAR-T therapy by Rakesh Awasthi, Harald J. Maier, Jie Zhang, Stephen Lim

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Anderson-Fabry Disease: From Endothelial Dysfunction to Emerging Therapies by Cosimo A. Stamerra, Rita Del Pinto, Paolo di Giosia, Claudio Ferri, Amirhossein Sahebkar

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Overview of Solid Lipid Nanoparticles in Breast Cancer Therapy by Kyumin Mo, Ayoung Kim, Soohyun Choe, Miyoung Shin, Hyunho Yoon

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Creeping Through the Backdoor: Disruption in Medicine and Health by Brendan Shaw, Brendan Shaw, Brendan Shaw, Orin Chisholm

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Novel therapies for proliferative retinopathies by Juan Manuel Martinez-Alejo, Leopoldo Martin Baiza-Duran, Juan de Dios Quintana-Hau

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CRISPR-Cas9 delivery strategies with engineered extracellular vesicles by Yaoyao Lu, Kelly Godbout, Gabriel Lamothe, Jacques P. Tremblay

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