Search Results - "gene therapies"

Mechanisms of manganese-induced neurotoxicity and the pursuit of neurotherapeutic strategies by Edward Pajarillo, Ivan Nyarko-Danquah, Alexis Digman, Harpreet Kaur Multani, Sanghoon Kim, Patric Gaspard, Michael Aschner, Eunsook Lee

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Treatment of Cystic Fibrosis: From Gene- to Cell-Based Therapies by Katelin M. Allan, Katelin M. Allan, Nigel Farrow, Nigel Farrow, Nigel Farrow, Martin Donnelley, Martin Donnelley, Martin Donnelley, Adam Jaffe, Adam Jaffe, Adam Jaffe, Shafagh A. Waters, Shafagh A. Waters, Shafagh A. Waters

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Polydopamine surface-modified nanocarriers for improved anticancer activity: Current progress and future prospects by Sandip M. Honmane, Manoj S. Charde, Sachin S. Salunkhe, Prafulla B. Choudhari, Sopan N. Nangare

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CRISPR-Cas9-mediated homology-directed repair for precise gene editing by Hongyu Liao, Jiahao Wu, Nathan J. VanDusen, Yifei Li, Yanjiang Zheng

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Engineering lentivirus envelope VSV-G for liver targeted delivery of IDOL-shRNA to ameliorate hypercholesterolemia and atherosclerosis by Wei Wang, Xuemei Chen, Jiali Chen, Menglong Xu, Ying Liu, Shijie Yang, Wenfeng Zhao, Shuhua Tan

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Suprachoroidal Injection: A Novel Approach for Targeted Drug Delivery by Kevin Y. Wu, Jamie K. Fujioka, Tara Gholamian, Marian Zaharia, Simon D. Tran

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MicroRNA-206 Downregulation Improves Therapeutic Gene Expression and Motor Function in mdx Mice by Karen Bulaklak, Bin Xiao, Chunping Qiao, Jianbin Li, Tejash Patel, Quan Jin, Juan Li, Xiao Xiao

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Riboswitches for Controlled Expression of Therapeutic Transgenes Delivered by Adeno-Associated Viral Vectors by Zachary J. Tickner, Michael Farzan

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Bcl-2 Overexpression Improves Survival and Efficacy of Neural Stem Cell-Mediated Enzyme Prodrug Therapy by Rachael Mooney, Asma Abdul Majid, Daniel Mota, Adam He, Soraya Aramburo, Linda Flores, Jennifer Covello-Batalla, Diana Machado, Joanna Gonzaga, Karen S. Aboody

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A Mixed-Surface Polyamidoamine Dendrimer for In Vitro and In Vivo Delivery of Large Plasmids by Bhairavi Srinageshwar, Maria Florendo, Brittany Clark, Kayla Johnson, Nikolas Munro, Sarah Peruzzaro, Aaron Antcliff, Melissa Andrews, Alexander Figacz, Douglas Swanson, Gary L. Dunbar, Ajit Sharma, Julien Rossignol

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Instrumental Activities of Daily Living Tools in Very-Low Vision: Ready for Use in Trials? by Jan Henrik Terheyden, David J. Fink, Susanne G. Pondorfer, Frank G. Holz, Robert P. Finger

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Precise engineering of Gemcitabine prodrug cocktails into single polymeric nanoparticles delivery for metastatic thyroid cancer cells by Chenggong Liu, Qiongmei Han, Hua Liu, Cuirong Zhu, Wei Gui, Xiaodong Yang, Wansen Li

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Roles of biomaterials in modulating the innate immune response in ocular therapy by Mehrnoosh Rafiei, Mehrnoosh Rafiei, Jin Teng Chung, Ying Chau

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Logic-gated tumor-microenvironment nanoamplifier enables targeted delivery of CRISPR/Cas9 for multimodal cancer therapy by Yongchun Pan, Xiaowei Luan, Fei Zeng, Xuyuan Wang, Shurong Qin, Qianglan Lu, Guanzhong He, Yanfeng Gao, Xiaolian Sun, Xin Han, Bangshun He, Yujun Song

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Potent Inhibition of HIV-1 Reverse Transcriptase and Replication by Nonpseudoknot, "UCAA-motif" RNA Aptamers by Angela S Whatley, Mark A Ditzler, Margaret J Lange, Elisa Biondi, Andrew W Sawyer, Jonathan L Chang, Joshua D Franken, Donald H Burke

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Aggravation of Cardiovascular and Respiratory Decline in Advanced Duchenne Muscular Dystrophy Complicated by Dilated Cardiomyopathy - Case Study and Review of Literature by Iwona Welian-Polus, Bartosz Mazur, Michał Bielak, Magdalena Mazur, Elżbieta Rypulak, Wiktoria Wilanowska, Anna Greguła, Karol Stachyrak, Dawid Mika, Kamila Turek

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CRISPR-based editing strategies to rectify EYA1 complex genomic rearrangement linked to haploinsufficiency by Hwalin Yi, Yejin Yun, Won Hoon Choi, Hye-Yeon Hwang, Ju Hyuen Cha, Heeyoung Seok, Jae-Jin Song, Jun Ho Lee, Sang-Yeon Lee, Daesik Kim

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A complex molecular landscape to drug delivery concept for achieving precise therapy in psoriasis by Krishna Yadav, Kantrol Kumar Sahu, Sucheta, Renu Yadav, Wasim Raza, Sunita Minz, Manju Rawat Singh, Deependra Singh, Madhulika Pradhan

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Discovery of peptides for ligand-mediated delivery of mRNA lipid nanoparticles to cystic fibrosis lung epithelia by Melissa R. Soto, Mae M. Lewis, Jasmim Leal, Yuting Pan, Rashmi P. Mohanty, Arian Veyssi, Esther Y. Maier, Brittany J. Heiser, Debadyuti Ghosh

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Delivery of DNA-Based Therapeutics for Treatment of Chronic Diseases by Carleigh Sussman, Rachel A. Liberatore, Marek M. Drozdz

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