Search Results - "gene therapies"

Designed U7 snRNAs inhibit DUX4 expression and improve FSHD-associated outcomes in DUX4 overexpressing cells and FSHD patient myotubes by Afrooz Rashnonejad, Gholamhossein Amini-Chermahini, Noah K. Taylor, Nicolas Wein, Scott Q. Harper

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The Law and Science Trial: a learning experience through role-playing by Santiago Castañeda Palacio, Laura Herrera-Almanza, Alejandro Hernández Martínez, Yuban Sebastian Cuartas-Agudelo, Lina Maria Martinez-Sanchez

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Development of a trilipid-based liposome system as a delivery vector for plasmid DNA in an MCF-7 cell line: Preparation, optimization, physical characterization and In Vitro cytoto... by Gloria Yi Wei Tseu, Khairul Azfar Kamaruzaman

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Layered Double Hydroxide as a Potent Non-viral Vector for Nucleic Acid Delivery Using Gene-Activated Scaffolds for Tissue Regeneration Applications by Lara S. Costard, Domhnall C. Kelly, Rachael N. Power, Christopher Hobbs, Sonia Jaskaniec, Valeria Nicolosi, Brenton L. Cavanagh, Caroline M. Curtin, Fergal J. O'Brien

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Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report by Inmaculada Pitarch Castellano, Eduardo López Briz, Eugenia Ibáñez Albert, Cristina Aguado Codina, Teresa Sevilla, José L. Poveda Andrés

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Cell-Penetrating Peptide and siRNA-Mediated Therapeutic Effects on Endometriosis and Cancer In Vitro Models by Kristina Kiisholts, Kaido Kurrikoff, Piret Arukuusk, Ly Porosk, Maire Peters, Andres Salumets, Ülo Langel

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Antisense Oligonucleotide-Based Therapy on miR-181a-5p Alleviates Cartilage Degradation of Temporomandibular Joint Osteoarthritis via Promoting SIRT1 by Hexu Qi, Zhenxing Zhao, Zhenxing Zhao, Lin Xu, Yue Zhang, Yifei Li, Li Xiao, Yu Li, Zhihe Zhao, Jie Fang

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Novel reporter mouse models useful for evaluating in vivo gene editing and for optimization of methods of delivering genome editing tools by Hiromi Miura, Jurai Imafuku, Aki Kurosaki, Masahiro Sato, Yongjie Ma, Guisheng Zhang, Akiko Mizutani, Kenya Kamimura, Channabasavaiah B. Gurumurthy, Dexi Liu, Masato Ohtsuka

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Transcription Factor Binding Site in Promoter Determines the Pattern of Plasmid-Based Transgene Expression In Vivo by Chunbo Zhang, Dexi Liu

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Ultrasonographic Development of the Fetal Sheep Stomach and Evaluation of Early Gestation Ultrasound-guided In Utero Intragastric Injection by Anna L. David, Khalil N. Abi-Nader, Boaz Weisz, S.W. Steven Shaw, Michael Themis, Terence Cook, Charles Coutelle, Charles H. Rodeck, Donald M. Peebles

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Protection from cisplatin-induced hearing loss with lentiviral vector-mediated ectopic expression of the anti-apoptotic protein BCL-XL by Larissa Nassauer, Hinrich Staecker, Peixin Huang, Bryan Renslo, Madeleine Goblet, Jennifer Harre, Athanasia Warnecke, Juliane W. Schott, Michael Morgan, Melanie Galla, Axel Schambach

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Gene transfer to rat cerebral cortex mediated by polysorbate 80 and poloxamer 188 nonionic surfactant vesicles by Attia N, Mashal M, Soto-Sánchez C, Martinez-Navarrete G., Fernández E, Grijalvo S, Eritja R, Puras G, Pedraz JL

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Advances in research to restore vision by Kun Do Rhee

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Application Perspectives of Nanomedicine in Cancer Treatment by Shanshan Hou, Muhammad Hasnat, Ziwei Chen, Yinong Liu, Mirza Muhammad Faran Ashraf Baig, Fuhe Liu, Zelong Chen

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Congenital epidermolysis bullosa: modern methods of diagnosis and therapy. Prospects for regenerative medicine by Alexey A. Kubanov, Arfenya E. Karamova, Ekaterina S. Monchakovskaya

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Results and possible prospects of genetic technology in ophthalmology (literature review). Part I by N. A. Gavrilova, O. Ie. Tishchenko, A. V. Zinov'eva

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Gene Silencing and Editing Strategies for Neurodegenerative Diseases by Clévio Nóbrega

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Diagnosis and Emerging Treatment Strategies for Mucopolysaccharidosis VII (Sly Syndrome) by Poswar FDO, Henriques Nehm J, Kubaski F, Poletto E, Giugliani R

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Bone Morphogenetic Protein 7 Gene Delivery Improves Cardiac Structure and Function in a Murine Model of Diabetic Cardiomyopathy by Mitchel Tate, Mitchel Tate, Nimna Perera, Nimna Perera, Darnel Prakoso, Darnel Prakoso, Darnel Prakoso, Andrew M. Willis, Minh Deo, Minh Deo, Osezua Oseghale, Hongwei Qian, Daniel G Donner, Daniel G Donner, Helen Kiriazis, Helen Kiriazis, Miles J. De Blasio, Miles J. De Blasio, Miles J. De Blasio, Miles J. De Blasio, Paul Gregorevic, Paul Gregorevic, Paul Gregorevic, Paul Gregorevic, Rebecca H. Ritchie, Rebecca H. Ritchie, Rebecca H. Ritchie

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Focused Ultrasound-Mediated Disruption of the Blood-Brain Barrier for AAV9 Delivery in a Mouse Model of Huntington's Disease by Bernie S. Owusu-Yaw, Yongzhi Zhang, Lilyan Garrett, Alvin Yao, Kai Shing, Ana Rita Batista, Miguel Sena-Esteves, Jaymin Upadhyay, Kimberly Kegel-Gleason, Nick Todd

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