Search Results - "gene therapies"

In utero therapy for congenital disorders using amniotic fluid stem cells. by Durrgah Latchumi Ramachandra, Sheng-Wen Steven eShaw, Sheng-Wen Steven eShaw, Panicos eShangaris, Stavros eLoukogeorgakis, Pascale V Guillot, Pascale V Guillot, Paolo eDe Coppi, Anna L David

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GENE DOPING IN SPORT - PERSPECTIVES AND RISKS by E Brzeziańska, D Domańska, A Jegier

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High-affinity RNA Aptamers Against the HIV-1 Protease Inhibit Both In Vitro Protease Activity and Late Events of Viral Replication by Sonald Duclair, Archana Gautam, Andrew Ellington, Vinayaka R Prasad

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Efficient Treatment of Rheumatoid Arthritis by Degradable LPCE Nano-Conjugate-Delivered p65 siRNA by Xiaohua Chen, Bailing Zhou, Yan Gao, Kaiyu Wang, Jieping Wu, Ming Shuai, Ke Men, Xingmei Duan

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Ensemble-Learning and Feature Selection Techniques for Enhanced Antisense Oligonucleotide Efficacy Prediction in Exon Skipping by Alex Zhu, Shuntaro Chiba, Yuki Shimizu, Katsuhiko Kunitake, Yasushi Okuno, Yoshitsugu Aoki, Toshifumi Yokota

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Current and Novel Emerging Medical Therapies for Peripheral Artery Disease: A Literature Review by AmirAhmad Arabzadeh, Elnaz Faghfuri, Saiedeh Razi Soofiyani, Elaheh Dalir Abdolahinia, Samaneh Siapush, Kazem Nejati-Koshki, Bita Shahrami, Vahid Asghariazar, Yasamin Pahlavan

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Design and Validation of a Process Based on Cationic Niosomes for Gene Delivery into Novel Urine-Derived Mesenchymal Stem Cells by Yerai Vado, Gustavo Puras, Melania Rosique, Cesar Martin, Jose Luis Pedraz, Shifa Jebari-Benslaiman, Marian M. de Pancorbo, Jon Zarate, Guiomar Perez de Nanclares

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Safety and Efficacy of Turoctocog Alfa in the Prevention and Treatment of Bleeding Episodes in Previously Treated Patients from China with Severe Hemophilia A: Results from the Gua... by Wu R, Sun J, Xu W, Hu Q, Li W, Xiao J, Yang F, Zeng X, Zeng Y, Zhou J, Matytsina I, Zhang S, Pluta M, Yang R

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Non-Viral Gene Delivery Systems by Henrique Faneca

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The future of non-viral gene delivery for the treatment of inherited retinal diseases by Jyoti Sharma, Eleftherios I. Paschalis

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Lenalidomide as potential treatment in small cell neuroendocrine lung cancer with del 5q by Paul Hartel

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Embelin, a small molecule quinone with a co-clinical power for castrate-resistant prostate cancer by Dr. Radhika J Poojari

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Innovating spinal muscular atrophy models in the therapeutic era by Ilaria Signoria, W. Ludo van der Pol, Ewout J. N. Groen

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Drug Delivery of siRNA Therapeutics

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Hearing Loss and Oxidative Stress: A Comprehensive Review by A. Maniaci, L. La Via, J. R. Lechien, G. Sangiorgio, G. Iannella, G. Magliulo, A. Pace, Q. Mat, S. Lavalle, M. Lentini

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Potential Therapeutic Strategies for Skeletal Muscle Atrophy by Li Huang, Ming Li, Chunyan Deng, Jiayi Qiu, Kexin Wang, Mengyuan Chang, Songlin Zhou, Yun Gu, Yuntian Shen, Wei Wang, Ziwei Huang, Hualin Sun

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Differential effects of SARM1 inhibition in traumatic glaucoma and EAE optic neuropathies by Pingting Liu, Wei Chen, Haowen Jiang, Haoliang Huang, Liping Liu, Fang Fang, Liang Li, Xue Feng, Dong Liu, Roopa Dalal, Yang Sun, Paymaan Jafar-Nejad, Karen Ling, Frank Rigo, Jiangbin Ye, Yang Hu

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Viral Vector-Based Delivery of CRISPR/Cas9 and Donor DNA for Homology-Directed Repair in an In Vitro Model for Canine Hemophilia B by Jian Gao, Thorsten Bergmann, Wenli Zhang, Maren Schiwon, Eric Ehrke-Schulz, Anja Ehrhardt

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Ultrasound‐microbubble cavitation facilitates adeno‐associated virus mediated cochlear gene transfection across the round‐window membrane by Zhen Zhang, Zhengnong Chen, Liqiang Fan, Thomas Landry, Jeremy Brown, Zhiping Yu, Shankai Yin, Jian Wang

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A pH- and Bioreducible Cationic Copolymer with Amino Acids and Piperazines for Adenovirus Delivery by Thavasyappan Thambi, Jeongmin Lee, A-Rum Yoon, Dayananda Kasala, Chae-Ok Yun

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