Search Results - "gene therapies"

Antisense Oligonucleotides against miR-21 Inhibit the Growth and Metastasis of Colorectal Carcinoma via the DUSP8 Pathway by Tao Ding, Panpan Cui, Ya Zhou, Chao Chen, Juanjuan Zhao, Hairong Wang, Mengmeng Guo, Zhixu He, Lin Xu

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Development of Tailor-Made Dendrimer Ternary Complexes for Drug/Gene Co-Delivery in Cancer by Ana Raquel Neves, Tânia Albuquerque, Rúben Faria, Milan Paul, Swati Biswas, Ângela Sousa, Diana Costa

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Lentivector Integration Sites in Ependymal Cells From a Model of Metachromatic Leukodystrophy: Non-B DNA as a New Factor Influencing Integration by Robert G McAllister, Jiahui Liu, Matthew W Woods, Sean K Tom, C Anthony Rupar, Stephen D Barr

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Identification of long non-coding RNA-related and -coexpressed mRNA biomarkers for hepatocellular carcinoma by Fan Zhang, Linda Ding, Li Cui, Robert Barber, Bin Deng

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Small molecule inhibitors target multiple neuropathological signaling to exert novel neuroprotection in intracranial aneurysms by Acharya Balkrishna, Shalini Mishra, Maneesha Rana, Satyendra Kumar Rajput, Suhrud Pathak, Keyi Liu, Muralikrishnan Dhanasekaran, Vedpriya Arya, Shalini Singh

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Changes in Ventilatory Support Requirements of Spinal Muscular Atrophy (SMA) Patients Post Gene-Based Therapies by Panagiota Panagiotou, Christina Kanaka-Gantenbein, Athanasios G. Kaditis

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Optimization of Critical Hairpin Features Allows miRNA-based Gene Knockdown Upon Single-copy Transduction by Renier Myburgh, Ophélie Cherpin, Erika Schlaepfer, Hubert Rehrauer, Roberto F Speck, Karl-Heinz Krause, Patrick Salmon

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Pedunculopontine Nucleus Degeneration Contributes to Both Motor and Non-Motor Symptoms of Parkinson's Disease by Nicole Elaine Chambers, Kathryn Lanza, Christopher Bishop

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Lipopolyplex-Mediated Co-Delivery of Doxorubicin and FAK siRNA to Enhance Therapeutic Efficiency of Treating Colorectal Cancer by Tilahun Ayane Debele, Chi-Kang Chen, Lu-Yi Yu, Chun-Liang Lo

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Attualità in nefrologia pediatrica: le conoscenze di rilievo per il nefrologo dell'adulto by Alberto Edefonti, Antonio Vergori, Giovanni Montini, Francesco Emma

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Gene Editing for the Efficient Correction of a Recurrent COL7A1 Mutation in Recessive Dystrophic Epidermolysis Bullosa Keratinocytes by Cristina Chamorro, Angeles Mencía, David Almarza, Blanca Duarte, Hildegard Büning, Jessica Sallach, Ingrid Hausser, Marcela Del Río, Fernando Larcher, Rodolfo Murillas

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Improved Lentiviral Gene Delivery to Mouse Liver by Hydrodynamic Vector Injection through Tail Vein by Trine Dalsgaard, Claudia R. Cecchi, Anne Louise Askou, Rasmus O. Bak, Pernille O. Andersen, David Hougaard, Thomas G. Jensen, Frederik Dagnæs-Hansen, Jacob Giehm Mikkelsen, Thomas J. Corydon, Lars Aagaard

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Peptide-Functionalized Dendrimer Nanocarriers for Targeted Microdystrophin Gene Delivery by Jessica Hersh, José Manuel Condor Capcha, Camila Iansen Irion, Guerline Lambert, Mauricio Noguera, Mohit Singh, Avinash Kaur, Emre Dikici, Joaquín J. Jiménez, Lina A. Shehadeh, Sylvia Daunert, Sapna K. Deo

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Pilot Program of Newborn Screening for 5q Spinal Muscular Atrophy in the Russian Federation by Kristina Mikhalchuk, Olga Shchagina, Alena Chukhrova, Viktoria Zabnenkova, Polina Chausova, Nina Ryadninskaya, Dmitry Vlodavets, Sergei I. Kutsev, Alexander Polyakov

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Experimental Disease-Modifying Agents for Frontotemporal Lobar Degeneration by Giunta M, Solje E, Gardoni F, Borroni B, Benussi A

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Survivin Clinical Features in Cervical Cancer by Miftakh Nur Rahman, Chyntia Resti Wijaya, Maria Novalentina

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Therapeutic effects of engineered exosome-based miR-25 and miR-181a treatment in spinocerebellar ataxia type 3 mice by silencing ATXN3 by Zhenchu Tang, Shenglan Hu, Ziwei Wu, Miao He

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DNM2 levels normalization improves muscle phenotypes of a novel mouse model for moderate centronuclear myopathy by Juliana de Carvalho Neves, Foteini Moschovaki-Filippidou, Johann Böhm, Jocelyn Laporte

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Nanotechnology in Pain Management by Andrew Torpey, Emily Bellow, Veronica Samojedny, Sukhpreet Ahluwalia, Amruta Desai, William Caldwell, Sergio Bergese

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Development of a Positive-readout Mouse Model of siRNA Pharmacodynamics by Mark Stevenson, Robert Carlisle, Ben Davies, Chris Preece, Michelle Hammett, Wei-li Liu, Kerry David Fisher, Amy Ryan, Heidi Scrable, Leonard William Seymour

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