Search Results - "gene therapies"

Reversal of experimental colitis disease activity in mice following administration of an adenoviral IL-10 vector by Ando Tomoaki, Wang Yuping, Jordan Paul, Jennings Merilyn H, Mathis J Michael, Sasaki Makoto, Joh Takashi, Alexander J Steven

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Nanomedicine in Central Nervous System (CNS) Disorders: A Present and Future Prospective by Shringika Soni, Rakesh Kumar Ruhela, Bikash Medhi

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Retrospectives on Three Decades of Safe Clinical Experience with Allogeneic Dermal Progenitor Fibroblasts: High Versatility in Topical Cytotherapeutic Care by Alexis Laurent, Marina Rey, Corinne Scaletta, Philippe Abdel-Sayed, Murielle Michetti, Marjorie Flahaut, Wassim Raffoul, Anthony de Buys Roessingh, Nathalie Hirt-Burri, Lee Ann Applegate

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Intracellular Delivery of Short Interfering RNA in Rat Organ of Corti Using a Cell-penetrating Peptide PepFect6 by Suvarna Dash-Wagh, Stefan Jacob, Staffan Lindberg, Anders Fridberger, Ülo Langel, Mats Ulfendahl

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Megakaryocyte membrane‐wrapped nanoparticles for targeted cargo delivery to hematopoietic stem and progenitor cells by Samik Das, Jenna C. Harris, Erica J. Winter, Chen‐Yuan Kao, Emily S. Day, Eleftherios Terry Papoutsakis

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Pharmacological treatment and BBB-targeted genetic therapy for MCT8-dependent hypomyelination in zebrafish by David Zada, Adi Tovin, Tali Lerer-Goldshtein, Lior Appelbaum

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RNA-Based Therapeutics: Current Developments in Targeted Molecular Therapy of Triple-Negative Breast Cancer by Sakib Haque, Kiri Cook, Gaurav Sahay, Conroy Sun

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Stimuli-Responsive Mesoporous Silica NPs as Non-viral Dual siRNA/Chemotherapy Carriers for Triple Negative Breast Cancer by Behrad Darvishi, Leila Farahmand, Keivan Majidzadeh-A

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Intratumoral electroporation of a self-amplifying RNA expressing IL-12 induces antitumor effects in mouse models of cancer by Noelia Silva-Pilipich, Aritz Lasarte-Cía, Teresa Lozano, Celia Martín-Otal, Juan José Lasarte, Cristian Smerdou

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Dendrimer-Coated Gold Nanoparticles for Efficient Folate-Targeted mRNA Delivery In Vitro by Londiwe Simphiwe Mbatha, Fiona Maiyo, Aliscia Daniels, Moganavelli Singh

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Exosome-based small RNA delivery: Progress and prospects by Mei Lu, Haonan Xing, Zhe Xun, Tianzhi Yang, Pingtian Ding, Cuifang Cai, Dongkai Wang, Xiaoyun Zhao

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Immune tolerance promotion by LSEC-specific lentiviral vector-mediated expression of the transgene regulated by the stabilin-2 promoter by Ester Borroni, Chiara Borsotti, Roberta A. Cirsmaru, Vakhtang Kalandadze, Rosella Famà, Simone Merlin, Brian Brown, Antonia Follenzi

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iRGD-Targeted Peptide Nanoparticles for Anti-Angiogenic RNAi-Based Therapy of Endometriosis by Anna Egorova, Mariya Petrosyan, Marianna Maretina, Elena Bazian, Iuliia Krylova, Vladislav Baranov, Anton Kiselev

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Context base editing for splice correction of IVSI-110 β-thalassemia by Basma Naiisseh, Panayiota L. Papasavva, Nikoletta Y. Papaioannou, Marios Tomazou, Lola Koniali, Xenia Felekis, Constantina G. Constantinou, Maria Sitarou, Soteroula Christou, Marina Kleanthous, Carsten W. Lederer, Petros Patsali

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Effective AAV-mediated gene replacement therapy in retinal organoids modeling AIPL1-associated LCA4 by Hali Sai, Bethany Ollington, Farah O. Rezek, Niuzheng Chai, Amelia Lane, Anastasios Georgiadis, James Bainbridge, Michel Michaelides, Almudena Sacristan-Reviriego, Pedro R.L. Perdigão, Amy Leung, Jacqueline van der Spuy

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Small interfering RNA delivery to the neurons near the amyloid plaques for improved treatment of Alzheimer׳s disease by Qian Guo, Xiaoyao Zheng, Peng Yang, Xiaoying Pang, Kang Qian, Pengzhen Wang, Shuting Xu, Dongyu Sheng, Liuchang Wang, Jinxu Cao, Wei Lu, Qizhi Zhang, Xinguo Jiang

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Evaluation of guide-free Cas9-induced genomic damage and transcriptome changes in pig embryos by Weikai Ge, Xiaozhu Zhao, Shixue Gou, Qin Jin, Fangbing Chen, Zhen Ouyang, Chengdan Lai, Tao Cui, Baoyi Mai, Sijia Lu, Kexin Zhong, Yanhui Liang, Tao Chen, Han Wu, Nan Li, Yinghua Ye, Liangxue Lai, Kepin Wang

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Formulation of Small Activating RNA Into Lipidoid Nanoparticles Inhibits Xenograft Prostate Tumor Growth by Inducing p21 Expression by Robert F Place, Ji Wang, Emily J Noonan, Rachel Meyers, Muthiah Manoharan, Klaus Charisse, Rick Duncan, Vera Huang, Xiaoling Wang, Long-Cheng Li

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Controlling neuropathic pain by adeno-associated virus driven production of the anti-inflammatory cytokine, interleukin-10 by Flotte Terence R, Maier Steven F, Hammack Sayamwong E, Wieseler-Frank Julie, Spataro Leah, Chacur Marucia, Cruz Pedro E, Langer Stephen J, Sloane Evan M, Milligan Erin D, Forsayeth John R, Leinwand Leslie A, Chavez Raymond, Watkins Linda R

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Insulinoma-Associated Protein 1 (INSM1): Diagnostic, Prognostic, and Therapeutic Use in Small Cell Lung Cancer by Renato Rocha, Rui Henrique

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