Search Results - "gene therapies"

Combined Antiviral Therapy Using Designed Molecular Scaffolds Targeting Two Distinct Viral Functions, HIV-1 Genome Integration and Capsid Assembly by Wannisa Khamaikawin, Somphot Saoin, Sawitree Nangola, Koollawat Chupradit, Supachai Sakkhachornphop, Sudarat Hadpech, Nattawat Onlamoon, Aftab A Ansari, Siddappa N Byrareddy, Pierre Boulanger, Saw-See Hong, Bruce E Torbett, Chatchai Tayapiwatana

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GlycoPEGylated recombinant factor IX for hemophilia B in context by Santagostino E, Mancuso ME

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The Modulatory Role of MicroRNA-873 in the Progression of KRAS-Driven Cancers by Hamada A. Mokhlis, Recep Bayraktar, Nashwa N. Kabil, Ayse Caner, Nermin Kahraman, Cristian Rodriguez-Aguayo, Erika P. Zambalde, Jianting Sheng, Kübra Karagoz, Pinar Kanlikilicer, Abdel Aziz H. Abdel Aziz, Tamer M. Abdelghany, Ahmed A. Ashour, Stephen Wong, Michael L. Gatza, George A. Calin, Gabriel Lopez-Berestein, Bulent Ozpolat

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Development of Lyophilized Gemini Surfactant-Based Gene Delivery Systems: Influence of Lyophilization on the Structure, Activity and Stability of the Lipoplexes by Waleed Mohammed-Saeid, Deborah Michel, Anas El-Aneed, Ronald E Verrall, Nicholas H Low, Ildiko Badea

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In silico methods for immunogenicity risk assessment and human homology screening for therapeutic antibodies by Aimee E. Mattei, Andres H. Gutierrez, Soorya Seshadri, Jacob Tivin, Matt Ardito, Amy S. Rosenberg, William D. Martin, Anne S. De Groot

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Keap1-Nrf2 Heterodimer: A Therapeutic Target to Ameliorate Sickle Cell Disease by Waseem Chauhan, Rahima Zennadi

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Anti-Cancer Effect of Neural Stem Cells Transfected with Carboxylesterase and sTRAIL Genes in Animals with Brain Lesions of Lung Cancer by Jung Hak Kim, Jae Sung Ahn, Dong-Seok Lee, Seok Ho Hong, Hong J. Lee

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Congenital Athymia: Unmet Needs and Practical Guidance by Howley E, Davies EG, Kreins AY

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Disposable Bioprocessing Systems by Niazi, Sarfaraz K.

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Design, synthesis and evaluation of VEGF-siRNA/CRS as a novel vector for gene delivery by Zhao W, Zhang YF, Jiang XY, Cui CY

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Evaluating meaningful changes in physical functioning and cognitive declines in metachromatic leukodystrophy: a caregiver interview study by Susan Martin, Nimanee Harris, Dorothy Romanus

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Early Changes in Tumor Perfusion from T1-Weighted Dynamic Contrast-Enhanced MRI following Neural Stem Cell-Mediated Therapy of Recurrent High-Grade Glioma Correlate with Overall Su... by Prativa Sahoo, Paul Frankel, Julie Ressler, Margarita Gutova, Alexander J. Annala, Behnam Badie, Jana Portnow, Karen S. Aboody, Massimo D'Apuzzo, Russell C. Rockne

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Molecular Genetics Analysis of 70 Chinese Families With Muscular Dystrophy Using Multiplex Ligation-Dependent Probe Amplification and Next-Generation Sequencing by Dong Wang, Min Gao, Kaihui Zhang, Ruifeng Jin, Yuqiang Lv, Yong Liu, Jian Ma, Ya Wan, Zhongtao Gai, Yi Liu

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Plasmid pORF-hTRAIL targeting to glioma using transferrin-modified polyamidoamine dendrimer by Gao S, Li J, Jiang C, Hong B, Hao B

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De novo variation in EP300 gene cause Rubinstein-Taybi syndrome 2 in a Chinese family with severe early-onset high myopia by Xiaoyu Huang, Xue Rui, Shuang Zhang, Xiaolong Qi, Weining Rong, Xunlun Sheng

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Spinal muscular atrophy - onasemnogene abeparvovec and other therapeutic options by Aleksandra Alicja Majchrzak-Celińska, Anna Warych, Mikołaj Szoszkiewicz

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Amelioration of Leigh syndrome induced by mouse blastocyst complementation with a mutant human mitochondrial ATP synthase 6 by Huijun Yuan, Keith A. Webster, Muhammad Tariq Bhatti, William W. Hauswirth, Alfred S. Lewin, John Guy

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The Utilization of RNA Silencing Technology to Mitigate the Voriconazole Resistance of Aspergillus Flavus; Lipofectamine-Based Delivery by Sanam Nami, Behzad Baradaran, Behzad Mansoori, Parivash Kordbacheh, Sasan Rezaie, Mehraban Falahati, Leila Mohamed Khosroshahi, Mahin Safara, Farideh Zaini

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Parents' dilemma: A therapeutic decision for children with spinal muscular atrophy (SMA) type 1 by Sophie Boursange, Sophie Boursange, Sophie Boursange, Marco Araneda, Caroline Stalens, Isabelle Desguerre, Isabelle Desguerre, Isabelle Desguerre, Christine Barnerias, Christine Barnerias, Christine Barnerias, Marie-Christine Nougues, Marie-Christine Nougues, Marie-Christine Nougues, Arnaud Isapof, Arnaud Isapof, Arnaud Isapof, Susana Quijano-Roy, Susana Quijano-Roy, Susana Quijano-Roy, Nadia Blu Genestine, Laetitia Ouillade, Maripaz Martinez Jalilie, Claudia Castiglioni, Odile Boespflug-Tanguy, Odile Boespflug-Tanguy, Odile Boespflug-Tanguy, Odile Boespflug-Tanguy, Marcela Gargiulo, Marcela Gargiulo, The SMAPAR Study Group

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Engineering the Escherichia coli Nitroreductase NfsA to Create a Flexible Enzyme-Prodrug Activation System by Abigail V. Sharrock, Abigail V. Sharrock, Abigail V. Sharrock, Sarah P. McManaway, Michelle H. Rich, Jeff S. Mumm, Ian F. Hermans, Ian F. Hermans, Ian F. Hermans, Moana Tercel, Moana Tercel, Frederik B. Pruijn, Frederik B. Pruijn, David F. Ackerley, David F. Ackerley, David F. Ackerley

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