Search Results - "gene therapies"

Elevated Intraocular Pressure and Glaucomatous Optic Neuropathy: Genes to Disease Mechanisms, Therapeutic Drugs, and Gene Therapies by Najam A. Sharif

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Fetal Therapies and Maternal-Fetal Tolerance by Tippi MacKenzie

Subjects: “…fetal gene therapy…”
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Chapter From the Molecular Biology to the Gene Therapy of a DNA Repair Syndrome: Fanconi Anemia by Bueren, Juan A.

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Dual-Acting Antiangiogenic Gene Therapy Reduces Inflammation and Regresses Neovascularization in Diabetic Mouse Retina by Rute S. Araújo, Diogo B. Bitoque, Gabriela A. Silva

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Episomal Nonviral Gene Therapy Vectors Slow Progression of Atherosclerosis in a Model of Familial Hypercholesterolemia by Alastair G Kerr, Lawrence CS Tam, Ashley B Hale, Milena Cioroch, Gillian Douglas, Keith M Channon, Richard Wade-Martins

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Cell and gene therapy regulatory, pricing, and reimbursement framework: With a focus on South Korea and the EU by SungKyung Lee, Jong Hyuk Lee

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RNA-Based Antipsoriatic Gene Therapy: An Updated Review Focusing on Evidence from Animal Models by Lin ZC, Hung CF, Aljuffali IA, Lin MH, Fang JY

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The world's first topical gene therapy drug for epidermolysis bullosa patients has been approved by article Editorial

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Hepatocyte-targeting and microenvironmentally responsive glycolipid-like polymer micelles for gene therapy of hepatitis B by Jing Miao, Xiqin Yang, Xuwei Shang, Zhe Gao, Qian Li, Yun Hong, Jiaying Wu, Tingting Meng, Hong Yuan, Fuqiang Hu

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The comparison of ZFNs, TALENs, and SpCas9 by GUIDE-seq in HPV-targeted gene therapy by Zifeng Cui, Hui Liu, Hongfeng Zhang, Zhaoyue Huang, Rui Tian, Lifang Li, Weiwen Fan, Yili Chen, Lijie Chen, Sen Zhang, Bhudev C. Das, Konstantin Severinov, Inga Isabel Hitzeroth, Priya Ranjan Debata, Zhuang Jin, Jiashuo Liu, Zheying Huang, Weiling Xie, Hongxian Xie, Bin Lang, Ji Ma, Haiyan Weng, Xun Tian, Zheng Hu

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Characterization of Recombinant Adeno-Associated Viruses (rAAVs) for Gene Therapy Using Orthogonal Techniques by Liam Cole, Diogo Fernandes, Maryam T. Hussain, Michael Kaszuba, John Stenson, Natalia Markova

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Cost-Effectiveness of a Hypothetical Gene Therapy for Alzheimer's Disease: A Markov Simulation Analysis by Thuy Chinh Kieu, Kevin Look

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Mesenchymal Stem Cells Engineered by Nonviral Vectors: A Powerful Tool in Cancer Gene Therapy by Yuan Ding, Chenyang Wang, Zhongquan Sun, Yingsheng Wu, Wanlu You, Zhengwei Mao, Weilin Wang

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Aerosol-Mediated Non-Viral Lung Gene Therapy: The Potential of Aminoglycoside-Based Cationic Liposomes by Tony Le Gall, Mathieu Berchel, Lee Davies, Angélique Mottais, Rosy Ghanem, Alain Fautrel, Deborah Gill, Steve Hyde, Pierre Lehn, Jean-Marie Lehn, Loïc Lemiègre, Thierry Benvegnu, Paul-Alain Jaffrès, Bruno Pitard, Tristan Montier

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New Perspectives of Gene Therapy on Polyglutamine Spinocerebellar Ataxias: From Molecular Targets to Novel Nanovectors by Fabiola V. Borbolla-Jiménez, María Luisa Del Prado-Audelo, Bulmaro Cisneros, Isaac H. Caballero-Florán, Gerardo Leyva-Gómez, Jonathan J. Magaña

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piggyBac as a high-capacity transgenesis and gene-therapy vector in human cells and mice by Rongbo Li, Yuan Zhuang, Min Han, Tian Xu, Xiaohui Wu

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Extracellular Vesicles as Delivery Vehicles for Therapeutic Nucleic Acids in Cancer Gene Therapy: Progress and Challenges by Rong Du, Chen Wang, Ling Zhu, Yanlian Yang

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Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C by Raimondo De Cristofaro

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Practical considerations relevant to treatment with the gene therapy beremagene geperpavec-svdt for dystrophic epidermolysis bullosa by Amy S. Paller, Shireen V. Guide, Diego Ayala, Mercedes E. Gonzalez, Anne W. Lucky, Isin Sinem Bagci, M. Peter Marinkovich

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Targeted Extracellular Vesicle Gene Therapy for Modulating Alpha-Synuclein Expression in Gut and Spinal Cord by Maria Izco, Martin Schleef, Marco Schmeer, Estefania Carlos, Guglielmo Verona, Lydia Alvarez-Erviti

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