Search Results - "oligonucleotide"

Musashi-2 contributes to myotonic dystrophy muscle dysfunction by promoting excessive autophagy through miR-7 biogenesis repression by Maria Sabater-Arcis, Ariadna Bargiela, Nerea Moreno, Javier Poyatos-Garcia, Juan J. Vilchez, Ruben Artero

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Enhancing peptide and PMO delivery to mouse airway epithelia by chemical conjugation with the amphiphilic peptide S10 by Maud Auger, Luis Sorroza-Martinez, Nadine Brahiti, Carole-Ann Huppé, Laurence Faucher-Giguère, Imen Arbi, Maxime Hervault, Xue Cheng, Bruno Gaillet, Frédéric Couture, David Guay, Al-Halifa Soultan

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Recent advances in β-thalassemias by Antonio Cao, Paolo Moi, Renzo Galanello

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A cell-penetrating peptide enhances delivery and efficacy of phosphorodiamidate morpholino oligomers in mdx mice by Li Gan, Leslie C.L. Wu, Jenna A. Wood, Monica Yao, Chris M. Treleaven, Nelsa L. Estrella, Bruce M. Wentworth, Gunnar J. Hanson, Marco A. Passini

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A novel DNA aptamer targeting lung cancer stem cells exerts a therapeutic effect by binding and neutralizing Annexin A2 by Yi-Ying Wu, I-Shan Hsieh, Chia-Hao Tung, Chen-Hsun Weng, Jia-En Wu, Jau-Song Yu, Tse-Ming Hong, Yuh-Ling Chen

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Structural variants and modifications of hammerhead ribozymes targeting influenza A virus conserved structural motifs by Tomasz Czapik, Julita Piasecka, Ryszard Kierzek, Elzbieta Kierzek

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Targets of the Entamoeba histolytica transcription factor URE3-BP. by Carol A Gilchrist, Duza J Baba, Yan Zhang, Oswald Crasta, Clive Evans, Elisabet Caler, Bruno W S Sobral, Christina B Bousquet, Megan Leo, Ameilia Hochreiter, Sarah K Connell, Barbara J Mann, William A Petri

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Subgenomic particles in rAAV vectors result from DNA lesion/break and non-homologous end joining of vector genomes by Junping Zhang, Ping Guo, Xiangping Yu, Dylan A. Frabutt, Anh K. Lam, Patrick L. Mulcrone, Matthew Chrzanowski, Jenni Firrman, Derek Pouchnik, Nianli Sang, Yong Diao, Roland W. Herzog, Weidong Xiao

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Single-swap editing for the correction of common Duchenne muscular dystrophy mutations by Andreas C. Chai, Francesco Chemello, Hui Li, Takahiko Nishiyama, Kenian Chen, Yu Zhang, Efraín Sánchez-Ortiz, Adeeb Alomar, Lin Xu, Ning Liu, Rhonda Bassel-Duby, Eric N. Olson

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Link between MHC Fiber Type and Restoration of Dystrophin Expression and Key Components of the DAPC by Tricyclo-DNA-Mediated Exon Skipping by Saleh Omairi, Kwan-Leong Hau, Henry Collin-Hooper, Federica Montanaro, Aurelie Goyenvalle, Luis Garcia, Ketan Patel

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Targeting ANGPTL3 by GalNAc-conjugated siRNA ANGsiR10 lowers blood lipids with long-lasting and potent efficacy in mice and monkeys by Jue Wang, Wen Zheng, Shuquan Zheng, Ye Yuan, Wei Wen, Weiyi Cui, Lifang Xue, Xueting Sun, Haibao Shang, Hongyan Zhang, Rui-Ping Xiao, Shan Gao, Xiuqin Zhang

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Development and validation of molecular markers for characterization of <it>Boehmeria nivea </it>var. <it>nivea </it>and <it>Boehmeria nivea </it>var. <it>tenacissima</it> by Lee Cheng-Yu, Tong Teng-Soung, Chiou Shu-Jiau, Li Chuan-I, Lee Lain-Tze, Cheng Ching-Ming

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Kinin B₁ and B₂ Receptors Contribute to Cisplatin-Induced Painful Peripheral Neuropathy in Male Mice by Gabriela Becker, Maria Fernanda Pessano Fialho, Indiara Brusco, Sara Marchesan Oliveira

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A novel gene therapy for methamphetamine- induced cognitive disorder with a hyper-acidified fusion variant of DnaJB1 by Mengru Zhang, Cheng Chen, Qingyan Peng, Xiaocong Wu, Ruiyi Zhou, Yuru Ma, Zhurong Zou

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Intranasal delivery: An attractive route for the administration of nucleic acid based therapeutics for CNS disorders by Pranav Shah, Manisha Lalan, Kalyani Barve

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Combination of protein and cell internalization SELEX identifies a potential RNA therapeutic and delivery platform to treat EphA2-expressing tumors by Laura Santana-Viera, Justin P. Dassie, Marta Rosàs-Lapeña, Silvia Garcia-Monclús, Mariona Chicón-Bosch, Marina Pérez-Capó, Lidia del Pozo, Sara Sanchez-Serra, Olga Almacellas-Rabaiget, Susana Maqueda-Marcos, Roser López-Alemany, William H. Thiel, Paloma H. Giangrande, Oscar M. Tirado

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The Aptamer Ob2, a novel AChE inhibitor, restores cognitive deficits and alleviates amyloidogenesis in 5×FAD transgenic mice by Zhiman Liang, Xin Li, Xiaoting Luo, Hongjie Luo, Yajun Chen, Mingliang Cai, Xinxin Zhong, Yingying Fang, Ting Guo, Yusheng Shi, Xingmei Zhang

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Cathepsin B deteriorates diabetic cardiomyopathy induced by streptozotocin via promoting NLRP3-mediated pyroptosis by Chen Liu, Qi Yao, Tongtong Hu, Zhulan Cai, Qingwen Xie, Jinhua Zhao, Yuan Yuan, Jian Ni, Qing Qing Wu

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The New Paradigms in Clinical Research: From Early Access Programs to the Novel Therapeutic Approaches for Unmet Medical Needs by Cristina Scavone, Gabriella di Mauro, Annamaria Mascolo, Liberato Berrino, Francesco Rossi, Annalisa Capuano

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A CAG repeat-targeting artificial miRNA lowers the mutant huntingtin level in the YAC128 model of Huntington's disease by Anna Kotowska-Zimmer, Lukasz Przybyl, Marianna Pewinska, Joanna Suszynska-Zajczyk, Dorota Wronka, Maciej Figiel, Marta Olejniczak

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