Sökresultat - Didu Kariyawasam
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Identification of Novel CSF-Derived miRNAs in Treated Paediatric Onset Spinal Muscular Atrophy: An Exploratory Study av Arlene M. D'Silva, Didu Kariyawasam, Pooja Venkat, Chelsea Mayoh, Michelle A. Farrar
Publicerad 2023Signum: Laddar…Connect to this object online.
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2
'Advocacy groups are the connectors': Experiences and contributions of rare disease patient organization leaders in advanced neurotherapeutics av Christina Q. Nguyen, Didu Kariyawasam, Kristine Alba‐Concepcion, Sarah Grattan, Kate Hetherington, Claire E. Wakefield, Susan Woolfenden, Russell C. Dale, Elizabeth E. Palmer, Michelle A. Farrar
Publicerad 2022Signum: Laddar…Connect to this object online.
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3
A contemporary analysis of the Australian clinical and genetic landscape of spinal muscular atrophy: a registry based studyResearch in context av Lakshmi Balaji, Robin Forbes, Anita Cairns, Hugo Sampaio, Andrew J. Kornberg, Lauren Sanders, Phillipa Lamont, Christina Liang, Kristi J. Jones, Kristen Nowak, Cullen O'Gorman, Ian Woodcock, Nancy Briggs, Eppie M. Yiu, Michelle A. Farrar, Didu Kariyawasam
Publicerad 2024Signum: Laddar…Connect to this object online.
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