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A contemporary analysis of the Australian clinical and genetic landscape of spinal muscular atrophy: a registry based studyResearch in context nork Lakshmi Balaji, Robin Forbes, Anita Cairns, Hugo Sampaio, Andrew J. Kornberg, Lauren Sanders, Phillipa Lamont, Christina Liang, Kristi J. Jones, Kristen Nowak, Cullen O'Gorman, Ian Woodcock, Nancy Briggs, Eppie M. Yiu, Michelle A. Farrar, Didu Kariyawasam
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