Search Results - Ludger Schöls
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1
Towards Personalized Allele-Specific Antisense Oligonucleotide Therapies for Toxic Gain-of-Function Neurodegenerative Diseases by Jacob Helm, Ludger Schöls, Stefan Hauser
Published 2022Call Number: Loading…Connect to this object online.
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2
Allele-specific targeting of mutant ataxin-3 by antisense oligonucleotides in SCA3-iPSC-derived neurons by Stefan Hauser, Jacob Helm, Melanie Kraft, Milena Korneck, Jeannette Hübener-Schmid, Ludger Schöls
Published 2022Call Number: Loading…Connect to this object online.
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3
Effective splicing restoration of a deep-intronic ABCA4 variant in cone photoreceptor precursor cells by CRISPR/SpCas9 approaches by Pietro De Angeli, Peggy Reuter, Stefan Hauser, Ludger Schöls, Katarina Stingl, Bernd Wissinger, Susanne Kohl
Published 2022Call Number: Loading…Connect to this object online.
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4
Antisense Oligonucleotide Mediated Splice Correction of a Deep Intronic Mutation in OPA1 by Tobias Bonifert, Irene Gonzalez Menendez, Florian Battke, Yvonne Theurer, Matthis Synofzik, Ludger Schöls, Bernd Wissinger
Published 2016Call Number: Loading…Connect to this object online.
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5
Human organoid model of pontocerebellar hypoplasia 2a recapitulates brain region-specific size differences by Theresa Kagermeier, Stefan Hauser, Kseniia Sarieva, Lucia Laugwitz, Samuel Groeschel, Wibke G. Janzarik, Zeynep Yentür, Katharina Becker, Ludger Schöls, Ingeborg Krägeloh-Mann, Simone Mayer
Published 2024Call Number: Loading…Connect to this object online.
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