Marina Cavazzana

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An Evaluation of Three Ways of Communicating Carrier Status Results to the Parents of Children in a Neonatal Sickle Cell Screening Programme by Christelle Rémus, Christelle Rémus, Christelle Rémus, Aurélie Stanislas, Aurélie Stanislas, Naïm Bouazza, Valérie Gauthereau, Michel Polak, Stéphane Blanche, Assa Niakaté, Eliane Gluckman, Jean-Marc Tréluyer, Arnold Munnich, Robert Girot, Robert Girot, Robert Girot, Marina Cavazzana, Marina Cavazzana
Published 2020Connect to this object online.
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Development of Lentiviral Vectors Simultaneously Expressing Multiple siRNAs Against CCR5, vif and tat/rev Genes for an HIV-1 Gene Therapy Approach by Francesca Spanevello, Arianna Calistri, Claudia Del Vecchio, Barbara Mantelli, Chiara Frasson, Giuseppe Basso, Giorgio Palù, Marina Cavazzana, Cristina Parolin
Published 2016Connect to this object online.
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4
Bayesian Modeling Immune Reconstitution Apply to CD34+ Selected Stem Cell Transplantation for Severe Combined Immunodeficiency by Jean-Sebastien Diana, Jean-Sebastien Diana, Naïm Bouazza, Naïm Bouazza, Chloe Couzin, Martin Castelle, Alessandra Magnani, Elisa Magrin, Jeremie Rosain, Jean-Marc Treluyer, Jean-Marc Treluyer, Capucine Picard, Capucine Picard, Despina Moshous, Despina Moshous, Stéphane Blanche, Stéphane Blanche, Bénédicte Neven, Bénédicte Neven, Marina Cavazzana, Marina Cavazzana
Published 2022Connect to this object online.
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Two Monogenetic Disorders, Activated PI3-Kinase-δ Syndrome 2 and Smith-Magenis Syndrome, in One Patient: Case Report and a Literature Review of Neurodevelopmental Impact in Primary... by Nidia Moreno-Corona, Nidia Moreno-Corona, Loïc Chentout, Loïc Chentout, Lucie Poggi, Lucie Poggi, Romane Thouenon, Romane Thouenon, Cecile Masson, Melanie Parisot, Lou Le Mouel, Capucine Picard, Capucine Picard, Capucine Picard, Isabelle André, Isabelle André, Marina Cavazzana, Marina Cavazzana, Laurence Perrin, Anne Durandy, Anne Durandy, Saba Azarnoush, Sven Kracker, Sven Kracker
Published 2021Connect to this object online.
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6
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies by Mégane Brusson, Anne Chalumeau, Pierre Martinucci, Oriana Romano, Tristan Felix, Valentina Poletti, Samantha Scaramuzza, Sophie Ramadier, Cecile Masson, Giuliana Ferrari, Fulvio Mavilio, Marina Cavazzana, Mario Amendola, Annarita Miccio
Published 2023Connect to this object online.
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7
Sustained remission after haploidentical bone marrow transplantation in a child with refractory systemic juvenile idiopathic arthritis by Guillaume Morelle, Martin Castelle, Graziella Pinto, Sylvain Breton, Matthieu Bendavid, Charlotte Boussard, Richard Mouy, Brigitte Bader-Meunier, Michaela Semeraro, Albert Faye, Marina Cavazzana, Bénédicte Neven, Stéphane Blanche, Pierre Quartier, Despina Moshous
Published 2021Connect to this object online.
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8
Limiting Thymic Precursor Supply Increases the Risk of Lymphoid Malignancy in Murine X-Linked Severe Combined Immunodeficiency by Samantha L. Ginn, Claus V. Hallwirth, Sophia H.Y. Liao, Erdahl T. Teber, Jonathan W. Arthur, Jianmin Wu, Hong Ching Lee, Szun S. Tay, Min Hu, Roger R. Reddel, Matthew P. McCormack, Adrian J. Thrasher, Marina Cavazzana, Stephen I. Alexander, Ian E. Alexander
Published 2017Connect to this object online.
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