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Differential effects of ELX/TEZ/IVA on organ-specific CFTR function in two patients with the rare CFTR splice mutations c.273+1G>A and c.165-2A>G by Sophia T. Pallenberg, Sophia T. Pallenberg, Inka Held, Christian Dopfer, Rebecca Minso, Rebecca Minso, Manuel M. Nietert, Gesine Hansen, Gesine Hansen, Burkhard Tümmler, Burkhard Tümmler, Anna-Maria Dittrich, Anna-Maria Dittrich
Published 2023Connect to this object online.
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Spirometric and anthropometric improvements in response to elexacaftor/tezacaftor/ivacaftor depending on age and lung disease severity by Katharina Schütz, Katharina Schütz, Sophia Theres Pallenberg, Sophia Theres Pallenberg, Julia Kontsendorn, David DeLuca, David DeLuca, Cinja Sukdolak, Cinja Sukdolak, Rebecca Minso, Rebecca Minso, Tina Büttner, Tina Büttner, Tina Büttner, Martin Wetzke, Christian Dopfer, Annette Sauer-Heilborn, Felix C. Ringshausen, Felix C. Ringshausen, Felix C. Ringshausen, Sibylle Junge, Burkhard Tümmler, Burkhard Tümmler, Gesine Hansen, Gesine Hansen, Anna-Maria Dittrich, Anna-Maria Dittrich
Published 2023Connect to this object online.
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3
Changes in cystic fibrosis transmembrane conductance regulator protein expression prior to and during elexacaftor-tezacaftor-ivacaftor therapy by Frauke Stanke, Frauke Stanke, Sophia T. Pallenberg, Stephanie Tamm, Stephanie Tamm, Silke Hedtfeld, Ella M. Eichhorn, Rebecca Minso, Gesine Hansen, Gesine Hansen, Tobias Welte, Tobias Welte, Annette Sauer-Heilborn, Felix C. Ringshausen, Felix C. Ringshausen, Sibylle Junge, Burkhard Tümmler, Burkhard Tümmler, Anna-Maria Dittrich, Anna-Maria Dittrich
Published 2023Connect to this object online.
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