Gaboxadol in Fragile X Syndrome: A 12-Week Randomized, Double-Blind, Parallel-Group, Phase 2a Study

• Main Authors: Dejan B. Budimirovic (Author), Kelli C. Dominick (Author), Lidia V. Gabis (Author), Maxwell Adams (Author), Mathews Adera (Author), Linda Huang (Author), Pamela Ventola (Author), Nicole R. Tartaglia (Author), Elizabeth Berry-Kravis (Author)
• Format: Book
• Published: Frontiers Media S.A., 2021-10-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Background: Fragile X syndrome (FXS), the most common single-gene cause of intellectual disability and autism spectrum disorder (ASD), is caused by a >200-trinucleotide repeat expansion in the 5' untranslated region of the fragile X mental retardation 1 (FMR1) gene. Individuals with FXS can...