Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Ubiquitylation as a Novel Pharmaceutical Target for Cystic Fibrosis

Mutations in the cystic fibrosis transmembrane conductance regulator (<i>CFTR)</i> gene decrease the structural stability and function of the CFTR protein, resulting in cystic fibrosis. Recently, the effect of CFTR-targeting combination therapy has dramatically increased, and it is expec...

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Main Authors: Ryosuke Fukuda (Author), Tsukasa Okiyoneda (Author)
Formato: Livro
Publicado em: MDPI AG, 2020-04-01T00:00:00Z.
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