Nusinersen in spinal muscular atrophy: Respiratory outcomes at tertiary care centers

• Main Authors: Fahad Alsohime (Author), Mohamad-Hani Temsah (Author), Muneera Al-Jelaify (Author), Hind Ali Bafaqih (Author), Kamal El Masri (Author), Ahmed Abusibah (Author), Ayman Al-Eyadhy (Author), Gamal Hasan (Author), Ali Alhaboob (Author), Majed Alabdulhafid (Author), Mohammed Abdulrahman Almazyad (Author), Abdulaziz Alghamdi (Author), Fahad A Bashiri (Author)
• Format: Book
• Published: Wolters Kluwer Medknow Publications, 2020-01-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Objectives: The objective of the study wasto describe the effect of nusinersen therapy and its 1st-year associated outcomes, weaning of ventilator support, and length of stay in pediatric intensive care among ventilator-dependent spinal muscular atrophy (SMA) patients. Methods: This is a multicenter...