Transferrin receptor-targeting property of pabinafusp alfa facilitates its uptake by various types of human brain-derived cells in vitro

Pabinafusp alfa, which is an anti-mucopolysaccharidosis II drug, consists of iduronate-2-sulfatase (IDS) genetically fused with an anti-transferrin receptor (TfR) antibody. While IDS is known to enter cells via mannose-6-phosphate receptor (M6PR)-mediated endocytosis, the anti-TfR antibody moiety of...

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Autors principals: Tomoki Fukatsu (Autor), Hanae Morio (Autor), Tomomi Furihata (Autor), Hiroyuki Sonoda (Autor)
Format: Llibre
Publicat: Frontiers Media S.A., 2023-07-01T00:00:00Z.
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