A RANDOMIZED, PLACEBO-CONTROLLED PHASE 3 STUDY OF OLEZARSEN IN PATIENTS WITH FAMILIAL CHYLOMICRONEMIA SYNDROME: THE BALANCE TRIAL
Therapeutic Area: Pharmacologic Therapy Background: Familial chylomicronemia syndrome (FCS) is a rare genetic disorder of lipoprotein lipase deficiency that results in severe hypertriglyceridemia and an increased risk of potentially life-threatening acute pancreatitis (AP). Decreasing high plasma le...
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Elsevier,
2024-09-01T00:00:00Z.
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