Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

• Main Authors: van Ommen Gert-Jan B (Author), Janson Anneke AM (Author), Aartsma-Rus Annemieke (Author), van Deutekom Judith CT (Author)
• Format: Book
• Published: BMC, 2007-07-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

<p>Abstract</p> <p>Background</p> <p>Antisense-mediated exon skipping is currently one of the most promising therapeutic approaches for Duchenne muscular dystrophy (DMD). Using antisense oligonucleotides (AONs) targeting specific exons the DMD reading frame is restored...