Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy
<p>Abstract</p> <p>Background</p> <p>Antisense-mediated exon skipping is currently one of the most promising therapeutic approaches for Duchenne muscular dystrophy (DMD). Using antisense oligonucleotides (AONs) targeting specific exons the DMD reading frame is restored...
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Main Authors: | van Ommen Gert-Jan B (Author), Janson Anneke AM (Author), Aartsma-Rus Annemieke (Author), van Deutekom Judith CT (Author) |
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Format: | Book |
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BMC,
2007-07-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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