Crowd Funding for Orphan Drugs: The Case of Baby Pia

Medical crowdfunding is a relatively new strategy to obtain access to orphan drugs. The case of Baby Pia, a Belgian girl with SMA type 1 for whom in 2018 more than $ 2.1 million was raised to get her treated with Zolgensma®, illustrates well the potential power of medical crowdfunding. But apart fro...

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Xehetasun bibliografikoak
Egile nagusia: Wim Pinxten (Egilea)
Formatua: Liburua
Argitaratua: Frontiers Media S.A., 2021-12-01T00:00:00Z.
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