Modelling the Cost-Effectiveness and Budget Impact of a Newborn Screening Program for Spinal Muscular Atrophy and Severe Combined Immunodeficiency

Spinal muscular atrophy (SMA) and severe combined immunodeficiency (SCID) are rare, inherited genetic disorders with severe mortality and morbidity. The benefits of early diagnosis and initiation of treatment are now increasingly recognized, with the most benefits in patients treated prior to sympto...

Full description

Saved in:
Bibliographic Details
Main Authors: Sophy T. F. Shih (Author), Elena Keller (Author), Veronica Wiley (Author), Michelle A. Farrar (Author), Melanie Wong (Author), Georgina M. Chambers (Author)
Format: Book
Published: MDPI AG, 2022-07-01T00:00:00Z.
Subjects:
Online Access:Connect to this object online.
Tags: Add Tag
No Tags, Be the first to tag this record!

Internet

Connect to this object online.

3rd Floor Main Library

Holdings details from 3rd Floor Main Library
Call Number: A1234.567
Copy 1 Available