Episomal Nonviral Gene Therapy Vectors Slow Progression of Atherosclerosis in a Model of Familial Hypercholesterolemia

Familial hypercholesterolemia (FH) is a life-threatening genetic disorder characterized by elevated levels of plasma low-density lipoprotein cholesterol (LDL-cholesterol). Current attempts at gene therapy for FH have been limited by the use of strong heterologous promoters which lack genomic DNA ele...

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Egile Nagusiak: Alastair G Kerr (Egilea), Lawrence CS Tam (Egilea), Ashley B Hale (Egilea), Milena Cioroch (Egilea), Gillian Douglas (Egilea), Keith M Channon (Egilea), Richard Wade-Martins (Egilea)
Formatua: Liburua
Argitaratua: Elsevier, 2016-01-01T00:00:00Z.
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